Table of Content
1 INTRODUCTION
1.1 OBJECTIVES OF THE STUDY
1.2 MARKET DEFINITION
1.3 OVERVIEW OF GLOBAL LEIGH SYNDROME TREATMENT MARKET
1.4 CURRENCY AND PRICING
1.5 LIMITATION
1.6 MARKETS COVERED
2 MARKET SEGMENTATION
2.1 KEY TAKEAWAYS
2.2 ARRIVING AT THE GLOBAL LEIGH SYNDROME TREATMENT MARKET SIZE
2.2.1 VENDOR POSITIONING GRID
2.2.2 TECHNOLOGY LIFE LINE CURVE
2.2.3 TRIPOD DATA VALIDATION MODEL
2.2.4 MARKET GUIDE
2.2.5 MULTIVARIATE MODELLING
2.2.6 TOP TO BOTTOM ANALYSIS
2.2.7 CHALLENGE MATRIX
2.2.8 APPLICATION COVERAGE GRID
2.2.9 STANDARDS OF MEASUREMENT
2.2.10 VENDOR SHARE ANALYSIS
2.2.11 DATA POINTS FROM KEY PRIMARY INTERVIEWS
2.2.12 DATA POINTS FROM KEY SECONDARY DATABASES
2.3 GLOBAL LEIGH SYNDROME TREATMENT MARKET: RESEARCH SNAPSHOT
2.4 ASSUMPTIONS
3 MARKET OVERVIEW
3.1 DRIVERS
3.2 RESTRAINTS
3.3 OPPORTUNITIES
3.4 CHALLENGES
4 EXECUTIVE SUMMARY
5 PREMIUM INSIGHTS
5.1 PESTEL ANALYSIS
5.2 PORTER’S FIVE FORCES MODEL
5.3 PATIENT NUMBER BY COUNNTRY
6 INDUSTRY INSIGHTS
6.1 MICRO AND MACRO ECONOMIC FACTORS
6.2 PENETRATION AND GROWTH PROSPECT MAPPING
6.3 KEY PRICING STRATEGIES
6.4 INTERVIEWS WITH SPECIALIST
6.5 ANALYIS AND RECOMMENDATION
7 INTELLECTUAL PROPERTY (IP) PORTFOLIO
7.1 PATENT QUALITY AND STRENGTH
7.2 PATENT FAMILIES
7.3 LICENSING AND COLLABORATIONS
7.4 COMPETITIVE LANDSCAPE
7.5 IP STRATEGY AND MANAGEMENT
7.6 OTHER
8 COST ANALYSIS BREAKDOWN
9 TECHNONLOGY ROADMAP
10 INNOVATION TRACKER AND STRATEGIC ANALYSIS
10.1 MAJOR DEALS AND STRATEGIC ALLIANCES ANALYSIS
10.1.1 JOINT VENTURES
10.1.2 MERGERS AND ACQUISITIONS
10.1.3 LICENSING AND PARTNERSHIP
10.1.4 TECHNOLOGY COLLABORATIONS
10.1.5 STRATEGIC DIVESTMENTS
10.2 NUMBER OF PRODUCTS IN DEVELOPMENT
10.3 STAGE OF DEVELOPMENT
10.4 TIMELINES AND MILESTONES
10.5 INNOVATION STRATEGIES AND METHODOLOGIES
10.6 RISK ASSESSMENT AND MITIGATION
10.7 FUTURE OUTLOOK
11 REGULATORY COMPLIANCE
11.1 REGULATORY AUTHORITIES
11.2 REGULATORY SUBMISSIONS
11.3 INTERNATIONAL HARMONIZATION
11.4 COMPLIANCE AND QUALITY MANAGEMENT SYSTEMS
11.5 REGULATORY CHALLENGES AND STRATEGIES
12 REIMBURSEMENT FRAMEWORK
13 OPPUTUNITY MAP ANALYSIS
14 VALUE CHAIN ANALYSIS
15 HEALTHCARE ECONOMY
15.1 HEALTHCARE EXPENDITURE
15.2 CAPITAL EXPENDITURE
15.3 CAPEX TRENDS
15.4 CAPEX ALLOCATION
15.5 FUNDING SOURCES
15.6 INDUSTRY BENCHMARKS
15.7 GDP RATION IN OVERALL GDP
15.8 HEALTHCARE SYSTEM STRUCTURE
15.9 GOVERNMENT POLICIES
15.1 ECONOMIC DEVELOPMENT
16 GLOBAL LEIGH SYNDROME TREATMENT MARKET, BY TYPE
16.1 OVERVIEW
16.2 MITOCHONDRIAL DNA-ASSOCIATED LEIGH SYNDROME
16.2.1 BY MUTATION TYPE
16.2.1.1. POINT MUTATIONS
16.2.1.2. DELETIONS
16.2.1.3. DUPLICATIONS
16.3 NUCLEAR GENE-ENCODED LEIGH SYNDROME
16.3.1 BY MUTATION TYPE
16.3.1.1. MISSENSE MUTATIONS
16.3.1.2. INSERTION/DELETION MUTATIONS
16.3.1.3. OTHERS
17 GLOBAL LEIGH SYNDROME TREATMENT MARKET, BY TREATMENT
17.1 OVERVIEW
17.2 MEDICATION
17.2.1 MEDICATIONS
17.2.1.1. DRUGS
17.2.1.1.1. BY TYPE
17.2.1.1.1.1 ANTIOXIDANTS
17.2.1.1.1.1.1. EPI-743
17.2.1.1.1.1.2. COENZYME Q10
17.2.1.1.1.1.3. OTHERS
17.2.1.1.1.2 ANTI-SEIZURE DRUGS
17.2.1.1.1.2.1. VALPROATE
17.2.1.1.1.2.2. LAMOTRIGINE
17.2.1.1.1.2.3. LEVETIRACETAM
17.2.1.1.1.2.4. OTHERS
17.2.1.1.1.3 MUSCLE RELAXANTS
17.2.1.1.1.4 OTHERS
17.2.1.1.2. BY DRUG TYPE
17.2.1.1.2.1 MARKETED
17.2.1.1.2.2 PIPELINE
17.2.1.1.2.2.1. EPI-743
17.2.1.1.2.2.2. (MTP-131)
17.2.1.1.2.2.3. KL1333
17.2.1.1.2.2.4. OTHERS
17.2.1.1.3. BY CLASS
17.2.1.1.3.1 BRANDED
17.2.1.1.3.2 GENERIC
17.2.2 GENE THERAPIES
17.3 THERAPY AND SUPPORTIVE TREATMENTS
17.3.1 DIETARY SUPPLEMENTS
17.3.1.1. VITAMIN B1 (THIAMINE)
17.3.1.2. VITAMIN B2 (RIBOFLAVIN)
17.3.1.3. COENZYME Q10
17.3.1.4. BIOTIN
17.3.1.5. LIPOIC ACID
17.3.1.6. OTHERS
17.3.2 KETOGENIC DIET
17.3.3 PHYSICAL AND OCCUPATIONAL THERAPY
17.3.4 RESPIRATORY SUPPORT
17.3.5 OTHERS
18 GLOBAL LEIGH SYNDROME TREATMENT MARKET, BY DIAGNOSIS
18.1 OVERVIEW
18.2 LABORATORY TESTS
18.2.1 BLOOD TESTS
18.2.1.1. LACTIC ACID (LACTATE) LEVELS
18.2.1.2. PYRUVATE LEVELS
18.2.1.3. OTHERS
18.2.2 CEREBROSPINAL FLUID (CSF) ANALYSIS
18.2.3 GENTIC TESTING
18.2.4 OTHERS
18.3 MRI
18.4 CT
18.5 OTHERS
19 GLOBAL LEIGH SYNDROME TREATMENT MARKET, BY AGE GROUP
19.1 OVERVIEW
19.2 INFANTS
19.3 TEENAGERS
19.4 ADULTS
20 GLOBAL LEIGH SYNDROME TREATMENT MARKET, BY ROUTE OF ADMINISTRATION
20.1 OVERVIEW
20.2 ORAL
20.2.1 TABLETS
20.2.2 CAPSULES
20.2.3 OTHERS
20.3 PARENTERAL
20.4 OTHERS
21 GLOBAL LEIGH SYNDROME TREATMENT MARKET, BY END-USERS
21.1 OVERVIEW
21.2 HOSPITALS
21.2.1 PUBLIC
21.2.2 PRIVATE
21.3 SPECIALTY CLINICS
21.4 HOMECARE
21.5 OTHERS
22 GLOBAL LEIGH SYNDROME TREATMENT MARKET, BY DISTRIBUTION CHANNEL
22.1 OVERVIEW
22.2 HOSPITAL PHARMACY
22.3 RETAIL PHARMACY
22.4 ONLINE PHARMACIES
22.5 OTHERS
23 GLOBAL LEIGH SYNDROME TREATMENT MARKET, COMPANY LANDSCAPE
23.1 COMPANY SHARE ANALYSIS: GLOBAL
23.2 COMPANY SHARE ANALYSIS: NORTH AMERICA
23.3 COMPANY SHARE ANALYSIS: EUROPE
23.4 COMPANY SHARE ANALYSIS: ASIA-PACIFIC
23.5 MERGERS & ACQUISITIONS
23.6 NEW PRODUCT DEVELOPMENT & APPROVALS
23.7 EXPANSIONS
23.8 REGULATORY CHANGES
23.9 PARTNERSHIP AND OTHER STRATEGIC DEVELOPMENTS
24 GLOBAL LEIGH SYNDROME TREATMENT MARKET, BY GEOGRAPHY
GLOBAL LEIGH SYNDROME TREATMENT MARKET, (ALL SEGMENTATION PROVIDED ABOVE IS REPRESENTED IN THIS CHAPTER BY COUNTRY)
24.1 NORTH AMERICA
24.1.1 U.S.
24.1.2 CANADA
24.1.3 MEXICO
24.2 EUROPE
24.2.1 GERMANY
24.2.2 FRANCE
24.2.3 U.K.
24.2.4 HUNGARY
24.2.5 LITHUANIA
24.2.6 AUSTRIA
24.2.7 IRELAND
24.2.8 NORWAY
24.2.9 POLAND
24.2.10 ITALY
24.2.11 SPAIN
24.2.12 RUSSIA
24.2.13 TURKEY
24.2.14 NETHERLANDS
24.2.15 SWITZERLAND
24.2.16 REST OF EUROPE
24.3 ASIA-PACIFIC
24.3.1 JAPAN
24.3.2 CHINA
24.3.3 SOUTH KOREA
24.3.4 INDIA
24.3.5 AUSTRALIA
24.3.6 SINGAPORE
24.3.7 THAILAND
24.3.8 MALAYSIA
24.3.9 INDONESIA
24.3.10 PHILIPPINES
24.3.11 VIETNAM
24.3.12 REST OF ASIA-PACIFIC
24.4 SOUTH AMERICA
24.4.1 BRAZIL
24.4.2 ARGENTINA
24.4.3 PERU
24.4.4 COLOMBIA
24.4.5 VENEZUELA
24.4.6 REST OF SOUTH AMERICA
24.5 MIDDLE EAST AND AFRICA
24.5.1 SOUTH AFRICA
24.5.2 SAUDI ARABIA
24.5.3 UAE
24.5.4 EGYPT
24.5.5 KUWAIT
24.5.6 ISRAEL
24.5.7 REST OF MIDDLE EAST AND AFRICA
24.6 KEY PRIMARY INSIGHTS: BY MAJOR COUNTRIES
25 GLOBAL LEIGH SYNDROME TREATMENT MARKET, SWOT AND DBMR ANALYSIS
26 GLOBAL LEIGH SYNDROME TREATMENT MARKET, COMPANY PROFILE
26.1 ELI LILLY AND COMPANY
26.1.1 COMPANY OVERVIEW
26.1.2 REVENUE ANALYSIS
26.1.3 GEOGRAPHIC PRESENCE
26.1.4 PRODUCT PORTFOLIO
26.1.5 RECENT DEVELOPMENTS
26.2 STEALTH BIOTHERAPEUTICS
26.2.1 COMPANY OVERVIEW
26.2.2 REVENUE ANALYSIS
26.2.3 GEOGRAPHIC PRESENCE
26.2.4 PRODUCT PORTFOLIO
26.2.5 RECENT DEVELOPMENTS
26.3 REATA PHARMACEUTICALS
26.3.1 COMPANY OVERVIEW
26.3.2 REVENUE ANALYSIS
26.3.3 GEOGRAPHIC PRESENCE
26.3.4 PRODUCT PORTFOLIO
26.3.5 RECENT DEVELOPMENTS
26.4 ASTELLAS PHARMA
26.4.1 COMPANY OVERVIEW
26.4.2 REVENUE ANALYSIS
26.4.3 GEOGRAPHIC PRESENCE
26.4.4 PRODUCT PORTFOLIO
26.4.5 RECENT DEVELOPMENTS
26.5 SANTHERA PHARMACEUTICALS
26.5.1 COMPANY OVERVIEW
26.5.2 REVENUE ANALYSIS
26.5.3 GEOGRAPHIC PRESENCE
26.5.4 PRODUCT PORTFOLIO
26.5.5 RECENT DEVELOPMENTS
26.6 BIOELECTRON TECHNOLOGY CORPORATION
26.6.1 COMPANY OVERVIEW
26.6.2 REVENUE ANALYSIS
26.6.3 GEOGRAPHIC PRESENCE
26.6.4 PRODUCT PORTFOLIO
26.6.5 RECENT DEVELOPMENTS
26.7 ABEONA THERAPEUTICS
26.7.1 COMPANY OVERVIEW
26.7.2 REVENUE ANALYSIS
26.7.3 GEOGRAPHIC PRESENCE
26.7.4 PRODUCT PORTFOLIO
26.7.5 RECENT DEVELOPMENTS
26.8 MINOVIA THERAPEUTICS
26.8.1 COMPANY OVERVIEW
26.8.2 REVENUE ANALYSIS
26.8.3 GEOGRAPHIC PRESENCE
26.8.4 PRODUCT PORTFOLIO
26.8.5 RECENT DEVELOPMENTS
26.9 ABLIVA AB
26.9.1 COMPANY OVERVIEW
26.9.2 REVENUE ANALYSIS
26.9.3 GEOGRAPHIC PRESENCE
26.9.4 PRODUCT PORTFOLIO
26.9.5 RECENT DEVELOPMENTS
26.1 GENSIGHT BIOLOGICS
26.10.1 COMPANY OVERVIEW
26.10.2 REVENUE ANALYSIS
26.10.3 GEOGRAPHIC PRESENCE
26.10.4 PRODUCT PORTFOLIO
26.10.5 RECENT DEVELOPMENTS
26.11 BRIDGEBIO PHARMAS
26.11.1 COMPANY OVERVIEW
26.11.2 REVENUE ANALYSIS
26.11.3 GEOGRAPHIC PRESENCE
26.11.4 PRODUCT PORTFOLIO
26.11.5 RECENT DEVELOPMENTS
26.12 PFIZER INC.
26.12.1 COMPANY OVERVIEW
26.12.2 REVENUE ANALYSIS
26.12.3 GEOGRAPHIC PRESENCE
26.12.4 PRODUCT PORTFOLIO
26.12.5 RECENT DEVELOPMENTS
26.13 TAKEDA PHARMACEUTICAL COMPANY LIMITED
26.13.1 COMPANY OVERVIEW
26.13.2 REVENUE ANALYSIS
26.13.3 GEOGRAPHIC PRESENCE
26.13.4 PRODUCT PORTFOLIO
26.13.5 RECENT DEVELOPMENTS
NOTE: THE COMPANIES PROFILED IS NOT EXHAUSTIVE LIST AND IS AS PER OUR PREVIOUS CLIENT REQUIREMENT. WE PROFILE MORE THAN 100 COMPANIES IN OUR STUDY AND HENCE THE LIST OF COMPANIES CAN BE MODIFIED OR REPLACED ON REQUEST
27 RELATED REPORTS
28 QUESTIONNAIRE
29 ABOUT DATA BRIDGE MARKET RESEARCH
