Image

Global N-Acetylglutamate Synthase Deficiency Market – Industry Trends and Forecast to 2030

Pharmaceutical

Image

Global N-Acetylglutamate Synthase Deficiency Market – Industry Trends and Forecast to 2030

  • Pharmaceutical
  • Upcoming Report
  • Dec 2022
  • Global
  • 350 Pages
  • No of Tables: 220
  • No of Figures: 60

Global N-Acetylglutamate Synthase Deficiency Market – Industry Trends and Forecast to 2030

Market Size in USD Billion

CAGR :  % Diagram

Diagram Forecast Period 2022–2030
Diagram Market Size (Base Year) USD 1.30 USD Billion
Diagram Market Size (Forecast Year) USD 1.71 USD Billion
Diagram CAGR %

Major Markets Players

  • Dummy1
  • Dummy2
  • Dummy3
  • Dummy4
  • Dummy5

Global N-Acetylglutamate Synthase Deficiency Market, By Diagnosis (Genetic Testing, New-born Screening Others), Treatment (Medications, Alternative Treatment, Others), Drug Type (Branded, Generic), End-Users (Hospitals, Specialty Clinics, Others), Distribution Channel (Hospital Pharmacy, Retail Pharmacy, online Pharmacies and Others) – Industry Trends and Forecast to 2030.

N-Acetylglutamate Synthase Deficiency Market

N-Acetylglutamate Synthase Deficiency Market Analysis and Size

N-Acetylglutamate synthase deficiency is a type of rare deficiency which happens in around 1 in 30,000 birth. This deficiency affects female and male equally. This deficiency often go unrecognized, but these disorders are underdiagnosed, making it difficult to access the frequency of urea cycle disorders in the overall population. Neurological symptoms may be life-threatening and include seizures, stupor, and coma.  

Data Bridge Market Research analyses a growth rate in the N-acetylglutamate synthase deficiency market in the forecast period 2023-2030. The expected CAGR N-acetylglutamate synthase deficiency market is tend to be around 3.50% in the mentioned forecast period. The market was valued at USD 1.3 billion in 2022, and it would grow upto USD 1.71 billion by 2030. In addition to the market insights such as market value, growth rate, market segments, geographical coverage, market players, and market scenario, the market report curated by the Data Bridge Market Research team also includes in-depth expert analysis, patient epidemiology, pipeline analysis, pricing analysis, and regulatory framework.

N-Acetylglutamate Synthase Deficiency Market Scope and Segmentation

Report Metric

Details

Forecast Period

2023 to 2030

Base Year

2022

Historic Years

2021 (Customizable to 2015 - 2020)

Quantitative Units

Revenue in USD Billion, Volumes in Units, Pricing in USD

Segments Covered

Diagnosis (Genetic Testing, New-born Screening Others), Treatment (Medications, Alternative Treatment, Others), Drug Type (Branded, Generic), End-Users (Hospitals, Specialty Clinics, Others), Distribution Channel (Hospital Pharmacy, Retail Pharmacy, online Pharmacies and Others)

Countries Covered

U.S., Canada and Mexico in North America, Germany, France, U.K., Netherlands, Switzerland, Belgium, Russia, Italy, Spain, Turkey, Rest of Europe in Europe, China, Japan, India, South Korea, Singapore, Malaysia, Australia, Thailand, Indonesia, Philippines, Rest of Asia-Pacific (APAC) in the Asia-Pacific (APAC), Saudi Arabia, U.A.E, South Africa, Egypt, Israel, Rest of Middle East and Africa (MEA) as a part of Middle East and Africa (MEA), Brazil, Argentina and Rest of South America as part of South America

Market Players Covered

Recordati Rare Diseases (Italy), Children's National Hospital (U.S.), Icahn School of Medicine at Mount Sinai (U.S.), and Boston Children's Hospital (U.S.)

Market Opportunities

  • Increasing Demand For Hospitals

Market Definition

N-acetylglutamate synthetase (NAGS) deficiency is a rare type of genetic disorder that is typically characterized by complete or partial lack of the enzyme N-acetylglutamate synthetase. Excess ammonia travels to the CNS through the blood, leading to NAGS deficiency symptoms and physical findings. This synthetase is one of the six enzymes which play a major role in the breakdown and removal of nitrogen from the body. The lack of N-acetylglutamate synthetase (NAGS) enzyme causes excessive accumulation of nitrogen in the form of ammonia in the blood.  

N-Acetylglutamate Synthase Deficiency Market Dynamics

Drivers

  • Increasing Treatment Developments

The treatment of NAGS deficiency aims to prevent excessive ammonia from formingaims to prevent excessive ammonia from forming or removing excessive ammonia during a hyperammonemic episode. Several long-term therapy for NAGS deficiency can be combined with dietary restrictions and the stimulation of alternate methods of converting and excreting nitrogen from the body. For instance, the U.S. FDA approved the use of Carbaglu (carbamylglutamate) tablets in 2010 to decrease blood ammonia levels in patients with NAGS deficiency. Carbaglu is manufactured by Orphan Europe. Some of the individuals who take carbamylglutamic acid may still need to follow certain dietary restrictions and may receive supplemental arginine. The initiation of carbaglu therapy has minimized the vulnerability of severe hyperammonemic episodes.

Opportunities

  • Increasing Demand For Hospitals

Drug stores and hospitals are the major application segments of N-acetylglutamate synthase deficiency drugs. In 2015, the hospital segment dominated the global market with a share of more than 80% in revenue. The segment is estimated to witness major growth due to increasing healthcare expenditure and a growing number of patients suffering from life-threatening diseases

Restraints/Challenges

  • Lack of Awareness

For many decades, this deficiency disease is not much known in several parts of the world. The appropriate treatment for the disease and its associated applications are unaware to the people. Thus, it hampers the market growth.   

  • High Cost of Treatment Process

The enormous expenditure required for its treatment processes obstructs the market growth. Numerous market players make huge investments in manufacturing new and advanced treatment procedures to faster the recovery process and in return the cost is increased.

This N-acetylglutamate synthase deficiency market report provides details of new recent developments, trade regulations, import-export analysis, production analysis, value chain optimization, market share, impact of domestic and localized market players, analyses opportunities in terms of emerging revenue pockets, changes in market regulations, strategic market growth analysis, market size, category market growths, application niches and dominance, product approvals, product launches, geographic expansions, technological innovations in the market. To gain more info on the N-acetylglutamate synthase deficiency market contact Data Bridge Market Research for an Analyst Brief, our team will help you take an informed market decision to achieve market growth.

Global N-Acetylglutamate Synthase Deficiency Market Scope

The N-acetylglutamate synthase deficiency market is segmented on the basis of diagnosis, treatment, drug type, end-user distribution channel. The growth amongst these segments will help you analyze meagre growth segments in the industries and provide the users with a valuable market overview and market insights to help them make strategic decisions for identifying core market applications.

Diagnosis

  • Genetic Testing
  • New-born Screening Others

Treatment

  • Medications
  • Alternative Treatment
  • Others

Drug Type

  • Branded
  • Generic

End-Users

  • Hospitals
  • Specialty Clinics
  • Others

Distribution Channel

  • Hospital Pharmacy
  • Retail Pharmacy
  • Online Pharmacies
  • Others

N-Acetylglutamate Synthase Deficiency Market Regional Analysis/Insights

The N-acetylglutamate synthase deficiency market is analyzed and market size insights and trends are provided by diagnosis, treatment, drug type, end-user distribution channel as referenced above.

The major countries covered in the N-acetylglutamate synthase deficiency market report are the U.S., Canada and Mexico in North America, Germany, France, U.K., Netherlands, Switzerland, Belgium, Russia, Italy, Spain, Turkey, Rest of Europe in Europe, China, Japan, India, South Korea, Singapore, Malaysia, Australia, Thailand, Indonesia, Philippines, Rest of Asia-Pacific (APAC) in the Asia-Pacific (APAC), Saudi Arabia, U.A.E, South Africa, Egypt, Israel, Rest of Middle East and Africa (MEA) as a part of Middle East and Africa (MEA), Brazil, Argentina and Rest of South America as part of South America.

North America is dominating the market ue to the presence of high healthcare expenditure and research & development.

Asia-Pacific is considered to grow over the coming years due to increased advancement in the technology as well as growing healthcare expenditure.

The country section of the report also provides individual market impacting factors and changes in regulation in the market domestically that impacts the current and future trends of the market. Also, the presence and availability of global brands and their challenges faced due to large or scarce competition from local and domestic brands, impact of domestic tariffs and trade routes are considered while providing forecast analysis of the country data. 

Competitive Landscape and Global N-Acetylglutamate Synthase Deficiency Market Share Analysis

The N-acetylglutamate synthase deficiency market competitive landscape provides details by competitor. Details included are company overview, company financials, revenue generated, market potential, investment in research and development, new market initiatives, global presence, production sites and facilities, production capacities, company strengths and weaknesses, product launch, product width and breadth, application dominance. The above data points provided are only related to the companies' focus related to N-acetylglutamate synthase deficiency market.

Key players operating in the N-acetylglutamate synthase deficiency market include:

  • Recordati Rare Diseases (Italy)
  • Children's National Hospital (U.S.)
  • Icahn School of Medicine at Mount Sinai (U.S.)
  • Boston Children's Hospital (U.S.)


SKU-

Please fill in the below form for detailed Table of Content

By clicking the "Submit" button, you are agreeing to the Data Bridge Market Research Privacy Policy and Terms and Conditions

Please fill in the below form for detailed List of Table

By clicking the "Submit" button, you are agreeing to the Data Bridge Market Research Privacy Policy and Terms and Conditions

Please fill in the below form for detailed List of Figure

By clicking the "Submit" button, you are agreeing to the Data Bridge Market Research Privacy Policy and Terms and Conditions

Please fill in the below form for Infographics

By clicking the "Submit" button, you are agreeing to the Data Bridge Market Research Privacy Policy and Terms and Conditions

Research Methodology:

Data collection and base year analysis are done using data collection modules with large sample sizes. The stage includes obtaining market information or related data through various sources and strategies. It includes examining and planning all the data acquired from the past in advance. It likewise envelops the examination of information inconsistencies seen across different information sources. The market data is analysed and estimated using market statistical and coherent models. Also, market share analysis and key trend analysis are the major success factors in the market report. To know more, please request an analyst call or drop down your inquiry.

The key research methodology used by DBMR research team is data triangulation which involves data mining, analysis of the impact of data variables on the market and primary (industry expert) validation. Data models include Vendor Positioning Grid, Market Time Line Analysis, Market Overview and Guide, Company Positioning Grid, Patent Analysis, Pricing Analysis, Company Market Share Analysis, Standards of Measurement, Global versus Regional and Vendor Share Analysis. To know more about the research methodology, drop in an inquiry to speak to our industry experts.

Please fill in the below form for Research Methodology

By clicking the "Submit" button, you are agreeing to the Data Bridge Market Research Privacy Policy and Terms and Conditions

Customization Available:

Data Bridge Market Research is a leader in advanced formative research. We take pride in servicing our existing and new customers with data and analysis that match and suits their goal. The report can be customized to include price trend analysis of target brands understanding the market for additional countries (ask for the list of countries), clinical trial results data, literature review, refurbished market and product base analysis. Market analysis of target competitors can be analyzed from technology-based analysis to market portfolio strategies. We can add as many competitors that you require data about in the format and data style you are looking for. Our team of analysts can also provide you data in crude raw excel files pivot tables (Fact book) or can assist you in creating presentations from the data sets available in the report.

Please fill in the below form for Available Customization

By clicking the "Submit" button, you are agreeing to the Data Bridge Market Research Privacy Policy and Terms and Conditions

Get online access to the report on the World's First Market Intelligence Cloud

  • Interactive Data Analysis Dashboard
  • Company Analysis Dashboard for high growth potential opportunities
  • Research Analyst Access for customization & queries
  • Competitor Analysis with Interactive dashboard
  • Latest News, Updates & Trend analysis
  • Harness the Power of Benchmark Analysis for Comprehensive Competitor Tracking
Request for Demo

FREQUENTLY ASK QUESTIONS

The N-acetylglutamate synthase deficiency market was USD 1.3 billion in 2022.
The N-acetylglutamate synthase deficiency market is projected to grow at a CAGR of 3.50% during the forecast period of 2023-2030.
The N-acetylglutamate synthase deficiency market is segmented under these headlines Diagnosis, Treatment, Drug Type, End-Users, Distribution Channel
North America is dominating the market due to the presence of high healthcare expenditure and research & development.
Free Sample Report

CHOOSE LICENCE TYPE

  • 7000.00
  • 4800.00
  • 3000.00
  • 8000.00
  • 12000.00

Why Choose Us

Industry Coverage

DBMR works across the globe in multiple industries which equip us with knowledge across verticals and provide our clients with insights not only from their industry but how other industries will impact their ecosystem.

Regional Coverage

Coverage of Data Bridge is not restricted to developed or emerging economies. We work across the globe covering the largest array of countries where no other market research or business consulting firm has ever conducted research; creating growth opportunities for our clients in areas which are still unknown.

Technology Coverage

In today’s world, technology drives the market sentiment, so our vision is to provide our clients insights not only for developed technologies but upcoming and disrupting technological changes throughout the product lifecycle by enabling them with unforeseen opportunities in the market which will create disruption in their industry. This leads to innovation and our clients to come out as winners.

Goal Oriented Solutions

DBMR goal is to help our clients achieve their goals through our solutions; hence we formatively create the most appropriate solutions for our client needs, saving time and efforts for them to drive their grand strategies.

Unparallel Analyst Support

Our analysts take pride in our clients’ success. Unlike others, we believe in working along our clients to achieve their goals with 24 hours analyst support determining the correct needs and inspire innovation through service.

Banner

Client Testimonials