中東和非洲溶小體貯積症藥物市場規模、份額和趨勢分析報告-產業概況和2032年預測

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中東和非洲溶小體貯積症藥物市場規模、份額和趨勢分析報告-產業概況和2032年預測

  • Pharmaceutical
  • Published Report
  • Oct 2024
  • MEA
  • 350 页面
  • 桌子數: 146
  • 图号: 46

通过敏捷供应链咨询解决关税挑战

供应链生态系统分析现已成为 DBMR 报告的一部分

Middle East And Africa Lysosomal Storage Disorder Drugs Market

市场规模(十亿美元)

CAGR :  % Diagram

Chart Image USD 510.05 Million USD 928.67 Million 2024 2032
Diagram Forecast Period
2025 –2032
Diagram Market Size (Base Year)
USD 510.05 Million
Diagram Market Size (Forecast Year)
USD 928.67 Million
Diagram CAGR
%
Diagram Major Markets Players
  • Dummy1
  • Dummy2
  • Dummy3
  • Dummy4
  • Dummy5

中東和非洲溶小體貯積症藥物市場細分,按疾病類型戈謝氏症法布瑞氏症龐貝氏症、黏多醣貯積症 (MPS)、尼曼匹克症克拉伯氏症等)、類型(酵素替代療法 (ERT)、底物減少療法(SRT)、分子伴侶療法等)、藥物(伊米苷酶、阿加糖苷酶β、艾杜爾硫酸酶、阿葡糖苷酶α、維拉苷酶、塔利苷酶阿爾法、拉羅尼酶、阿加糖苷酶β、加洛硫酸酶、阿伐葡萄糖苷酶阿爾法靜脈注射 (IV)、皮下(SC)、口服等)、年齡層(兒科、成人和老年人)、性別(男性和女性)、分銷管道(醫院藥房、藥局)零售藥局和線上藥局)-產業趨勢及 2032 年預測

中東和非洲溶小體貯積症藥物市場

中東和非洲溶小體貯積症藥物市場分析

中東和非洲溶小體貯積症藥物市場涵蓋用於診斷、治療和管理各種溶酶體貯積症的藥物商業領域,溶酶體貯積症是一種罕見的遺傳疾病,通常以由於酶缺乏導致溶酶體內未消化物質的積累為特徵。該市場包括一系列治療產品,例如酶替代療法、底物減少療法和基因療法,旨在解決 LSD 的多種臨床表現,例如戈謝病、法布瑞氏症和龐貝氏症。隨著人們認識的不斷提高、研究和技術的進步以及新療法數量的不斷增加,這個市場有望大幅擴張。此外,醫療保健支出的增加和改善罕見疾病治療途徑的舉措進一步推動了市場成長,為製藥公司和醫療保健提供者帶來了機會和挑戰。

溶小體貯積症藥物市場規模

2024 年中東和非洲溶小體貯積症藥物市場規模為 5.1005 億美元,預計到 2032 年將達到 9.2867 億美元,在 2025 年至 2032 年的預測期內,複合年增長率為 7.8%。除了對市場價值、成長率、細分、地理覆蓋範圍和主要參與者等市場情景的洞察外,Data Bridge Market Research 策劃的市場報告還包括進出口分析、生產能力概覽、生產消費分析、價格趨勢分析、氣候變遷情境、供應鏈分析、價值鏈分析、原材料/消耗品概覽、供應商選擇標準、PESTLE 分析、波特分析和監管框架。

溶小體貯積症藥物市場趨勢

“溶小體貯積症治療的生物技術進展”

生物技術的進步在改變溶小體貯積症 (LSD) 治療前景方面發揮了關鍵作用,為患者提供了更有效、更個人化的治療選擇。酵素替代療法 (ERT) 透過直接解決導致溶酶體貯積症 (LSD) 的酵素缺乏症,徹底改變了疾病的治療方法。在 LSD 患者中,由於缺乏特定的酶,導致毒性物質在細胞中積聚,從而損害器官和組織。 ERT 透過使用合成酶來彌補缺失的酶,改善代謝功能並緩解症狀。多年來,ERT 取得了顯著進步,出現了新的、更有效的配方和輸送方法,可改善酵素的吸收並減少副作用。這些創新帶來了更好的臨床結果,減緩了疾病進展,減少了器官損傷,並提高了患者的生活品質。

報告範圍和溶小體貯積症藥物市場細分         

屬性

溶小體貯積症藥物關鍵市場洞察

涵蓋的領域

  • 疾病類型分類: 戈謝氏症法布瑞氏症、龐貝氏症、黏多醣貯積症(MPS)、尼曼匹克氏症、克拉伯氏症等
  • 按類型:酵素替代療法 (ERT)、底物減少療法 (SRT)、伴侶療法及其他
  • 依藥物分類:伊米苷酶、阿加糖苷酶β、艾杜爾硫酸酶、阿糖苷酶α、維拉苷酶、塔利苷酶α、拉羅尼酶、阿加糖苷酶α、加硫酶、阿伐葡萄糖苷酶α等
  • 依給藥途徑:靜脈注射 (IV)、皮下注射 (SC)、口服及其他
  • 依年齡層:兒童、成人和老年人
  • 按性別:男性和女性
  • 按分銷管道:  醫院藥房、藥局和零售藥房、網路藥房

覆蓋國家

南非、埃及、巴林、阿拉伯聯合大公國、科威特、阿曼、卡達、沙烏地阿拉伯以及中東和非洲其他地區

主要市場參與者

賽諾菲(法國)、BioMarin(美國)、輝瑞公司(美國)、Amicus Therapeutics, Inc.(美國)、武田藥品工業株式會社(日本)、Protalix BioTherapeutics Inc.(以色列)和 REGENXBIO INC.(美國)等

市場機會

  • 正在研發的藥物數量不斷增加
  • 越來越重視早期診斷

加值資料資訊集

除了對市場價值、成長率、細分、地理覆蓋範圍和主要參與者等市場情景的洞察之外,Data Bridge Market Research 策劃的市場報告還包括進出口分析、生產能力概覽、生產消費分析、價格趨勢分析、氣候變遷情景、供應鏈分析、價值鏈分析、原材料/消耗品概覽、供應商選擇標準、PESTLE 分析、波特分析和監管框架。

溶小體貯積症藥物市場定義

溶小體貯積症藥物是指專門為治療溶小體貯積症 (LSD) 而開發的一類藥物,溶小體貯積症是一組由負責分解溶小體內複雜分子的特定酵素缺乏所引起的罕見遺傳疾病。這些藥物旨在透過替換缺失的酵素(酵素替代療法)、增強身體產生酵素的能力或修改因酵素缺乏而累積的底物(底物減少療法)來解決與 LSD 相關的潛在代謝異常。透過改善酵素功能或減少底物的毒性積聚,這些治療可以緩解症狀,減緩疾病進展,並最終改善受這些具有挑戰性的疾病影響的個人的生活品質。

溶小體貯積症藥物市場動態

驅動程式  

  • 溶小體貯積症的新興個人化醫療

新興的個人化醫療透過提供針對患者個別基因特徵的治療,正在改變溶小體貯積症 (LSD) 的治療格局。 LSD 是由影響酶功能的基因突變引起的,而這些突變在患者之間可能存在很大差異。個人化治療包括分析患者獨特的基因組成,以發展更有針對性的治療方法,優化酵素替代或基因療法等療法的療效。這種精確度可以使治療更好地與患者的特定需求相匹配,最大限度地減少副作用並提高治療效果。隨著基因檢測和技術的進步,醫療保健提供者能夠確定最合適的干預措施,從而有可能提高反應率和整體治療成功率。個人化醫療的轉變正在加速客製化 LSD 治療的發展,這有望徹底改變疾病管理。隨著這些創新,全球溶小體貯積症藥物市場對更有效、個人化治療方案的需求不斷增加。因此,個人化醫療是市場成長的關鍵驅動力,因為它可以提高治療效果並改善患者預後,增強對治療方案的信心。

例如,

2023年2月,根據NCBI發表的文章,新興的個人化醫療利用個人的基因圖譜來指導與疾病的預防、診斷和治療相關的決策。這種方法可以更精確、有效地治療溶小體貯積症 (LSD),並針對特定的基因突變量身訂做治療方案。隨著個人化醫療變得越來越普遍,它推動了對標靶 LSD 療法的需求,從而促進了全球溶小體貯積症藥物市場的成長。

  • 增加政府對罕見疾病治療研究的資助

政府對罕見疾病治療研究的資助和撥款對於推動溶酶體貯積症 (LSD) 等疾病的治療方法的發展至關重要。罕見疾病由於患者數量少,往往缺乏商業可行性,為藥物開發帶來了重大挑戰。為了解決這個問題,世界各國政府正在加大資金投入,鼓勵這些服務不足地區的研究。以贈款、補貼和稅收抵免形式提供的財政支持可幫助製藥公司和研究機構克服開發罕見疾病治療方法的高成本和風險。此外,政府意識到解決方案的迫切需要,往往會加快這些治療的監管進程。透過減輕研究人員和公司的財務負擔,這些資助機制使得探索創新療法成為可能,例如酵素替代療法和基因療法,否則這些療法將面臨重大發展障礙。

例如,

2023年8月,根據美國國家罕見疾病組織發表的文章稱,美國國家罕見疾病組織宣佈為罕見疾病研究提供超過10萬美元的資助,凸顯了政府對推進治療的支持力度加大。這些資金使研究人員能夠探索溶酶體貯積症(LSD)等罕見疾病的創新療法。這種資金支持加速了藥物開發,透過培育新的治療選擇推動了全球 LSD 藥物市場的成長。         

機會

  • 正在研發的藥物數量不斷增加

溶小體貯積症 (LSD) 治療藥物數量的不斷增加為全球溶小體貯積症藥物市場帶來了重大機遇,有可能改善治療方案並提高患者的治療效果。隨著研究人員和製藥公司對這些疾病的了解不斷加深,他們正在開發各種新型療法,包括基因療法、底物減少療法和小分子藥物。這條擴展的產品線反映了人們對 LSD 領域未滿足的醫療需求的日益認識,並有望為患者提供更多適合其具體情況的治療方式。引入創新療法可以增強患者對治療的依從性,減輕疾病負擔,並最終改善患有這些疾病的個人的生活品質。

例如,

2024年6月,Ultragenyx宣布計畫申請加速核准UX111用於治療A型Sanfilippo症候群(MPS IIIA)。 UX111 是一種新型體內基因療法,目前處於 1/2/3 期開發階段,用於治療 A 型 Sanfilippo 症候群 (MPS IIIA),這是一種罕見的致命溶酶體貯積症,目前尚無核准的治療方法,主要影響中樞神經系統。

  • 越來越重視早期診斷

人們越來越重視溶小體貯積症 (LSD) 的早期診斷,這為全球溶小體貯積症藥物市場提供了重大機遇,因為可以促進及時幹預,從而大大改善患者的治療效果。隨著醫療保健系統透過改善篩檢計畫、基因檢測和診斷技術的進步更加重視早期發現,更多的患者可能會在疾病早期得到診斷。這種早期介入不僅可以更好地控制症狀,還可以提高現有和新興療法的潛在療效。這種轉變的結果是需要治療方案並可從中受益的患者群體更加廣泛,最終推動溶酶體貯積症藥物市場的需求。

例如,

2023 年 2 月,根據《溶小體貯積症:從生物學到臨床(以印度為參考)》一文,早期診斷是 LSD 管理中最關鍵的部分,因為它為治療幹預、精確的遺傳諮詢、產前診斷和患者更好的結果提供了機會。

限制/挑戰

  • 醫療專業人員和患者缺乏意識

醫療保健專業人員和患者對溶酶體貯積症 (LSD) 缺乏認識,這對早期診斷、治療和有效管理造成了重大障礙。許多醫療保健提供者,特別是在罕見疾病接觸有限的地區,往往未能認識到 LSD 的症狀,而 LSD 的症狀多種多樣,且與其他更常見的疾病有重疊。缺乏知識會導致診斷延遲、誤診和治療無效,加劇疾病的嚴重程度。對於患者,尤其是資源貧乏或服務不足地區的患者,缺乏意識會阻礙早期幹預,使他們不知道潛在的治療方法。 LSD 的複雜性和罕見性使情況更加複雜,因為患者和醫療保健專業人員可能無法完全理解早期治療的重要性或專門護理選擇的可用性。及時診斷和治療的患者減少,導致臨床結果不理想。這種缺乏認知限制了對 LSD 特定治療的需求,並阻礙了全球溶小體貯積症藥物市場的整體成長。

例如,

2024 年 1 月,根據 Wiley 發表的文章,由於臨床表型重疊和嚴重程度不同,成人 LSD 病例從出現症狀到確診通常有大約 15 年的顯著診斷延遲。這種延遲凸顯了醫療保健專業人員,特別是治療成年患者的專業人員缺乏意識。這些限制阻礙了早期發現和及時治療,限制了全球溶小體貯積症藥物市場的成長。

  • 藥品審批程序延長

冗長的藥物審批流程對溶小體貯積症藥物市場造成了重大限制,減緩了急需的治療方法的推出。獲得新藥監管批准的過程,特別是針對 LSD 等罕見疾病的藥物,涉及大量臨床試驗、大量文獻以及 FDA 和 EMA 等監管機構的嚴格評估。由於需要對安全性、有效性和潛在的長期影響進行全面評估,這些審批時間通常會延長。就 LSD 而言,這些疾病的罕見性和複雜性又增加了另一層挑戰,因為臨床試驗的患者數量有限,因此難以產生可靠的數據。這些罕見疾病需要專門的治療,而且缺乏既定的標準,這使得審批過程變得複雜。因此,藥物開發商面臨更長的等待期、新療法上市的延遲以及額外的成本,這可能會讓製藥公司感到沮喪。因此,冗長的審批流程減緩了患者獲得創新療法的速度,降低了市場成長速度,並阻礙了 LSD 有效治療的可近性。這種監管延遲最終對全球溶小體貯積症藥物市場造成了重大限制。

例如,

2024年8月,根據Drugs.com發表的文章,藥物的研究、開發和審批過程通常需要12至15年。這一延長的時間延遲了新療法的推出並增加了製藥公司的成本。因此,冗長的藥品審批流程限制了治療的普及速度,從而抑制了全球 LSD 藥物市場的成長。

本市場報告提供了最新發展、貿易法規、進出口分析、生產分析、價值鏈優化、市場份額、國內和本地化市場參與者的影響的詳細信息,分析了新興收入領域的機會、市場法規的變化、戰略市場增長分析、市場規模、類別市場增長、應用領域和主導地位、產品批准、產品發布、地理擴展、市場技術創新。要獲取更多市場信息,請聯繫 Data Bridge Market Research 獲取分析師簡報,我們的團隊將幫助您做出明智的市場決策,實現市場成長。

溶小體貯積症藥物市場範圍

市場根據疾病類型、類型、藥物、給藥途徑、年齡層、性別和分銷管道進行細分。這些細分市場之間的成長將幫助您分析行業中成長微弱的細分市場,並為用戶提供有價值的市場概覽和市場洞察,幫助他們做出策略決策,確定核心市場應用。

疾病類型

  •  戈謝氏症
    • 類型 1
    • 類型 3
    • 類型 2
  • 法布瑞氏症
  • 龐貝氏症
    • 嬰兒起搏泵
    • 晚髮型龐貝氏症
  • 黏多醣貯積症(MPS)
    • 黏多醣
    • 黏多醣體Ⅱ型
    • 黏多醣IV
    • 甲基磺酸六
    • 黏多醣III型
  • 尼曼匹克病
    • C型
    • B型
    • A型
  • 螃蟹病
  • 其他的

類型

  • 酵素替代療法(ERT)
  • 底物減少療法(SRT)
  • 伴侶治療
  • 其他的

藥物

  • 伊米苷酶
  • 阿加糖酶β
  • 艾杜爾硫酸酶
  • 阿爾法葡萄糖苷酶
  • 維拉苷酶
  • 塔利葡糖酶阿爾法
  • 拉羅尼酶
  • 阿加糖酶α
  • 加硫酸酶
  • 阿伐葡萄糖苷酶α
  • 其他的

給藥途徑

  • 靜脈注射(IV)
  • 皮下(SC)
  • 口服
  • 其他的

年齡組

  • 兒科
  • 成年人
  • 老年

性別

  • 男性
  • 女性

分銷管道

  • 醫院藥房
  • 藥局和零售藥房
  • 網路藥局

溶小體貯積症藥物市場區域分析

對市場進行分析,並根據上述疾病類型、類型、藥物、給藥途徑、年齡層、性別和分銷管道提供市場規模洞察和趨勢。

市場涵蓋的國家有南非、埃及、巴林、阿拉伯聯合大公國、科威特、阿曼、卡達、沙烏地阿拉伯以及中東和非洲其他國家。

沙烏地阿拉伯憑藉其先進的醫療基礎設施、高藥物採用率、大量的研發投入以及龐大的患者群體,有望成為中東和非洲溶酶體貯積症藥物市場中佔據主導地位並增長最快的國家。

報告的國家部分還提供了影響個別市場因素以及影響市場當前和未來趨勢的國內市場監管變化。下游和上游價值鏈分析、技術趨勢和波特五力分析、案例研究等數據點是用於預測各國市場情景的一些指標。此外,在對國家數據進行預測分析時,還考慮了中東和非洲品牌的存在和可用性,以及由於來自本地和國內品牌的大量或稀缺的競爭而面臨的挑戰、國內關稅和貿易路線的影響。

溶小體貯積症藥物市場份額

市場競爭格局提供了競爭對手的詳細資訊。詳細資訊包括公司概況、公司財務狀況、收入、市場潛力、研發投資、新市場計劃、中東和非洲業務、生產基地和設施、生產能力、公司優勢和劣勢、產品發布、產品寬度和廣度、應用優勢。以上提供的數據點僅與公司對市場的關注有關。

溶小體貯積症藥物市場領導者有:

  • 賽諾菲(法國)
  • BioMarin(美國)
  • 輝瑞公司(美國)
  • Amicus Therapeutics, Inc.(美國)
  • 武田藥品工業株式會社(日本)
  • Protalix BioTherapeutics Inc.(以色列)
  • REGENXBIO INC.(美國)

溶小體貯積症藥物市場的最新進展

  • 2024 年 10 月,Amicus Therapeutics 宣布就其治療法布瑞氏症的藥物 Galafold (migalastat) 達成和解。和解協議解決了正在進行的專利糾紛,並確認該藥品的營銷可以繼續,不受訴訟幹擾。這項與多方達成的協議旨在為 Galafold 的可用性和開發提供穩定性,同時保護智慧財產權
  • 2024 年 6 月,Amicus Therapeutics 因其用於治療法布瑞氏症的創新療法 Pombiliti(miglustat)榮獲英國 Prix Galien 獎。該獎項旨在表彰製藥創新領域的卓越成就,並強調龐比利蒂在改善罕見遺傳疾病患者生活方面所發揮的作用。這項榮譽彰顯了 Amicus 在罕見疾病治療領域的領導地位
  • 2024年4月,Forge Biologics宣布將在2024年5月舉行的ASGCT第27屆年會上進行9次演講,包括一次最新口頭報告和三次技術會議。演講將涵蓋製程開發、分子進展和臨床更新,包括 FBX-101 在克拉伯病治療中的顯著臨床結果
  • 2023年11月,凱西集團再次獲得義大利、澳洲、美國等多個地區的「卓越職場」認證。凱西的員工回覆率為 85%,整體滿意度為 83%,體現了其致力於營造積極、包容、協作的工作環境,並注重員工的福祉和成長
  • 2024 年 1 月,生物製藥公司 Denali Therapeutics Inc. 宣布了 2024 年的進展和里程碑。 Denali Therapeutics Inc. 是一家致力於開發跨越血腦屏障治療神經退化性疾病和溶酶體貯積症的療法的生物製藥公司。該公司執行長 Ryan Watts 博士於 1 月 9 日在第 42 屆摩根大通年度醫療保健大會的公司演講中重點介紹了這些進展。


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目录

1 INTRODUCTION

1.1 OBJECTIVES OF THE STUDY

1.2 MARKET DEFINITION

1.3 OVERVIEW OF MIDDLE EAST AND AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET

1.4 MARKETS COVERED

2 MARKET SEGMENTATION

2.1 MARKETS COVERED

2.2 GEOGRAPHICAL SCOPE

2.3 YEARS CONSIDERED FOR THE STUDY

2.4 CURRENCY AND PRICING

2.5 DBMR TRIPOD DATA VALIDATION MODEL

2.6 MULTIVARIATE MODELLING

2.7 PRIMARY INTERVIEWS WITH KEY OPINION LEADERS

2.8 DBMR MARKET POSITION GRID

2.9 SECONDARY SOURCES

2.1 ASSUMPTIONS

3 EXECUTIVE SUMMARY

4 PREMIUM INSIGHT

4.1 PORTER’S FIVE FORCES

4.2 PIPELINE ANALYSIS

5 MIDDLE EAST AND AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET: REGULATIONS

5.1 REGULATORY AUTHORITIES IN THE MIDDLE EAST AND AFRICA.

6 MARKET OVERVIEW

6.1 DRIVERS

6.1.1 BIOTECHNOLOGY ADVANCEMENTS FOR LYSOSOMAL STORAGE DISORDERS TREATMENTS

6.1.2 EMERGING PERSONALIZED MEDICINE FOR LYSOSOMAL STORAGE DISORDERS

6.1.3 INCREASED GOVERNMENT FUNDING FOR RESEARCH INTO RARE DISEASE TREATMENTS

6.1.4 COLLABORATIONS AND PARTNERSHIPS BETWEEN PHARMACEUTICAL COMPANIES AND RESEARCH INSTITUTIONS

6.2 RESTRAINTS

6.2.1 LACK OF AWARENESS AMONG HEALTHCARE PROFESSIONALS AND PATIENTS

6.2.2 PROLONGED DRUG APPROVAL PROCEDURES

6.3 OPPORTUNITIES

6.3.1 INCREASING NUMBER OF PIPELINE DRUGS

6.3.2 GROWING EMPHASIS ON EARLY DIAGNOSIS

6.3.3 ADVANCEMENTS IN GENE THERAPY FOR THE TREATMENT OF LYSOSOMAL STORAGE DISORDERS

6.4 CHALLENGES

6.4.1 SIGNIFICANT EXPENSES RELATED TO THE TREATMENT OF THE DISEASE

6.4.2 NARROW PATIENT BASE SUFFERING FROM LYSOSOMAL STORAGE DISORDERS

7 MIDDLE EAST AND AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY TYPE OF DISORDER

7.1 OVERVIEW

7.2 GAUCHER DISEASE

7.2.1 TYPE 1

7.2.2 TYPE 3

7.2.3 TYPE 2

7.3 FABRY DISEASE

7.4 POMPE DISEASE

7.4.1 INFANTILE-ONSET POMPE

7.4.2 LATE-ONSET POMPE

7.5 MUCOPOLYSACCHARIDOSIS (MPS)

7.5.1 MPS I

7.5.2 MPS II

7.5.3 MPS IV

7.5.4 MPS VI

7.5.5 MPS III

7.6 NIEMANN-PICK DISEASE

7.6.1 TYPE C

7.6.2 TYPE B

7.6.3 TYPE A

7.7 KRABBE DISEASE

7.8 OTHERS

8 MIDDLE EAST AND AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY DRUGS

8.1 OVERVIEW

8.2 IMIGLUCERASE

8.3 AGALSIDASE BETA

8.4 IDURSULFASE

8.5 ALGLUCOSIDASE ALPHA

8.6 VELAGLUCERASE

8.7 TALIGLUCERASE ALFA

8.8 LARONIDASE

8.9 AGALSIDASE ALPHA

8.1 GALSULFASE

8.11 AVALGLUCOSIDASE ALFA

8.12 OTHERS

9 MIDDLE EAST AND AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY TYPE

9.1 OVERVIEW

9.2 ENZYME REPLACEMENT THERAPY (ERT)

9.3 SUBSTRATE REDUCTION THERAPY (SRT)

9.4 CHAPERONE THERAPY

9.5 OTHERS

10 MIDDLE EAST AND AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY GENDER

10.1 OVERVIEW

10.2 MALE

10.3 FEMALE

11 MIDDLE EAST AND AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY AGE GROUP

11.1 OVERVIEW

11.2 PEDIATRIC

11.3 ADULT

11.4 GERIATRIC

12 MIDDLE EAST AND AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY DISTRIBUTION CHANNEL

12.1 OVERVIEW

12.2 HOSPITAL PHARMACIES

12.3 DRUGS STORES AND RETAIL PHARMACIES

12.4 ONLINE PHARMACIES

13 MIDDLE EAST AND AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY ROUTE OF ADMINISTRATION

13.1 OVERVIEW

13.2 INTRAVENOUS (IV)

13.3 SUBCUTANEOUS (SC)

13.4 ORAL

13.5 OTHERS

14 MIDDLE EAST AND AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY REGION

14.1 MIDDLE EAST AND AFRICA

14.1.1 SAUDI ARABIA

14.1.2 UNITED ARAB EMIRATES (UAE)

14.1.3 SOUTH AFRICA

14.1.4 EGYPT

14.1.5 QATAR

14.1.6 KUWAIT

14.1.7 OMAN

14.1.8 BAHRAIN

14.1.9 REST OF MIDDLE EAST AND AFRICA

15 MIDDLE EAST AND AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET: COMPANY LANDSCAPE

15.1 COMPANY SHARE ANALYSIS: MIDDLE EAST AND AFRICA

16 SWOT ANALYSIS

17 COMPANY PROFILES

17.1 SANOFI

17.1.1 COMPANY SNAPSHOT

17.1.2 REVENUE ANALYSIS

17.1.3 COMPANY SHARE ANALYSIS

17.1.4 PRODUCT PORTFOLIO

17.1.5 RECENT DEVELOPMENT

17.2 BIOMARIN

17.2.1 COMPANY SNAPSHOT

17.2.2 REVENUE ANALYSIS

17.2.3 COMPANY SHARE ANALYSIS

17.2.4 PRODUCT PORTFOLIO

17.2.5 RECENT DEVELOPMENT

17.3 PFIZER INC.

17.3.1 COMPANY SNAPSHOT

17.3.2 REVENUE ANALYSIS

17.3.3 COMPANY SHARE ANALYSIS

17.3.4 PRODUCT PORTFOLIO

17.3.5 RECENT DEVELOPMENT

17.4 TAKEDA PHARMACEUTICAL COMPANY LIMITED

17.4.1 COMPANY SNAPSHOT

17.4.2 REVENUE ANALYSIS

17.4.3 COMPANY SHARE ANALYSIS

17.4.4 PRODUCT PORTFOLIO

17.4.5 RECENT DEVELOPMENT

17.5 AMICUS THERAPEUTIC, INC.

17.5.1 COMPANY SNAPSHOT

17.5.2 REVENUE ANALYSIS

17.5.3 COMPANY SHARE ANALYSIS

17.5.4 PRODUCT PORTFOLIO

17.5.5 RECENT DEVELOPMENT

17.6 CHIESI FARMACEUTICI S.P.A.

17.6.1 COMPANY SNAPSHOT

17.6.2 PRODUCT PORTFOLIO

17.6.3 RECENT DEVELOPMENT

17.7 DENALI THERAPEUTICS

17.7.1 COMPANY SNAPSHOT

17.7.2 REVENUE ANALYSIS

17.7.3 PIPELINE PRODUCT PORTFOLIO

17.7.4 RECENT DEVELOPMENT

17.8 FORGE BIOLOGICS

17.8.1 COMPANY SNAPSHOT

17.8.2 PIPELINE PRODUCT PORTFOLIO

17.8.3 RECENT DEVELOPMENT

17.9 JCR PHARMACEUTICALS CO., LTD.

17.9.1 COMPANY SNAPSHOT

17.9.2 REVENUE ANALYSIS

17.9.3 PINELINE PRODUCT PORTFOLIO

17.9.4 PRODUCT PORTFOLIO

17.9.5 RECENT DEVELOPMENT

17.1 ORCHARD THERAPEUTICS PLC

17.10.1 COMPANY SNAPSHOT

17.10.2 REVENUE ANALYSIS

17.10.3 PRODUCT PORTFOLIO

17.10.4 RECENT DEVELOPMENT

17.11 PROTALIX BIOTHERAPEUTICS

17.11.1 COMPANY SNAPSHOT

17.11.2 REVENUE ANALYSIS

17.11.3 PIPELINE PRODUCT PORTFOLIO

17.11.4 RECENT DEVELOPMENT

17.12 REGENXBIO INC.

17.12.1 COMPANY SNAPSHOT

17.12.2 REVENUE ANALYSIS

17.12.3 PINELINE PRODUCT PORTFOLIO

17.12.4 RECENT DEVELOPMENT

17.13 SANGAMO THERAPEUTICS

17.13.1 COMPANY SNAPSHOT

17.13.2 REVENUE ANALYSIS

17.13.3 PRODUCT PORTFOLIO

17.13.4 RECENT DEVELOPMENT

17.14 SPUR THERAPEUTICS

17.14.1 COMPANY SNAPSHOT

17.14.2 PRODUCT PORTFOLIO

17.14.3 RECENT DEVELOPMENT

17.15 ULTRAGENYX PHARMACEUTICAL INC.

17.15.1 COMPANY SNAPSHOT

17.15.2 REVENUE ANALYSIS

17.15.3 PRODUCT PORTFOLIO

17.15.4 RECENT DEVELOPMENT

18 QUESTIONNAIRE

19 RELATED REPORTS

表格列表

TABLE 1 MIDDLE EAST AND AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY TYPE OF DISORDER, 2018-2032 (USD MILLION)

TABLE 2 MIDDLE EAST AND AFRICA GAUCHER DISEASE IN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY REGION, 2018-2032(USD MILLION)

TABLE 3 MIDDLE EAST AND AFRICA GAUCHER DISEASE IN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY TYPE, 2018-2032 (USD MILLION)

TABLE 4 MIDDLE EAST AND AFRICA FABRY DISEASE IN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY REGION, 2018-2032 (USD MILLION)

TABLE 5 MIDDLE EAST AND AFRICA POMPE DISEASE IN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY REGION, 2018-2032 (USD MILLION)

TABLE 6 MIDDLE EAST AND AFRICA POMPE DISEASE IN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY TYPE, 2018-2032 (USD MILLION)

TABLE 7 MIDDLE EAST AND AFRICA MUCOPOLYSACCHARIDOSIS (MPS) IN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY REGION, 2018-2032 (USD MILLION)

TABLE 8 MIDDLE EAST AND AFRICA MUCOPOLYSACCHARIDOSIS (MPS) IN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY TYPE, 2018-2032 (USD MILLION)

TABLE 9 MIDDLE EAST AND AFRICA NIEMANN-PICK DISEASE IN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY REGION, 2018-2032 (USD MILLION)

TABLE 10 MIDDLE EAST AND AFRICA NIEMANN-PICK DISEASE IN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY TYPE, 2018-2032 (USD MILLION)

TABLE 11 MIDDLE EAST AND AFRICA KRABBE DISEASE IN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY REGION, 2018-2032 (USD MILLION)

TABLE 12 MIDDLE EAST AND AFRICA OTHERS IN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY REGION, 2018-2032 (USD MILLION)

TABLE 13 MIDDLE EAST AND AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY DRUGS, 2018-2032 (USD MILLION)

TABLE 14 MIDDLE EAST AND AFRICA IMIGLUCERASE IN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY REGION, 2018-2032(USD MILLION)

TABLE 15 MIDDLE EAST AND AFRICA AGALSIDASE BETA IN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY REGION, 2018-2032 (USD MILLION)

TABLE 16 MIDDLE EAST AND AFRICA IDURSULFASE IN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY REGION, 2018-2032 (USD MILLION)

TABLE 17 MIDDLE EAST AND AFRICA ALGLUCOSIDASE ALPHA IN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY REGION, 2018-2032 (USD MILLION)

TABLE 18 MIDDLE EAST AND AFRICA VELAGLUCERASE IN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY REGION, 2018-2032 (USD MILLION)

TABLE 19 MIDDLE EAST AND AFRICA TALIGLUCERASE ALFA IN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY REGION, 2018-2032 (USD MILLION)

TABLE 20 MIDDLE EAST AND AFRICA LARONIDASE IN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY REGION, 2018-2032 (USD MILLION)

TABLE 21 MIDDLE EAST AND AFRICA AGALSIDASE ALPHA IN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY REGION, 2018-2032 (USD MILLION)

TABLE 22 MIDDLE EAST AND AFRICA GALSULFASE IN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY REGION, 2018-2032 (USD MILLION)

TABLE 23 MIDDLE EAST AND AFRICA AVALGLUCOSIDASE ALFA IN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY REGION, 2018-2032 (USD MILLION)

TABLE 24 MIDDLE EAST AND AFRICA OTHERS IN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY REGION, 2018-2032 (USD MILLION)

TABLE 25 MIDDLE EAST AND AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY TYPE, 2018-2032 (USD MILLION)

TABLE 26 MIDDLE EAST AND AFRICA ENZYME REPLACEMENT THERAPY (ERT) IN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY REGION, 2018-2032(USD MILLION)

TABLE 27 MIDDLE EAST AND AFRICA SUBSTRATE REDUCTION THERAPY (SRT) IN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY REGION, 2018-2032 (USD MILLION)

TABLE 28 MIDDLE EAST AND AFRICA CHAPERONE THERAPY IN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY REGION, 2018-2032 (USD MILLION)

TABLE 29 MIDDLE EAST AND AFRICA OTHERS IN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY REGION, 2018-2032 (USD MILLION)

TABLE 30 MIDDLE EAST AND AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY GENDER, 2018-2032 (USD MILLION)

TABLE 31 MIDDLE EAST AND AFRICA MALE IN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY REGION, 2018-2032 (USD MILLION)

TABLE 32 MIDDLE EAST AND AFRICA FEMALE IN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY REGION, 2018-2032 (USD MILLION)

TABLE 33 MIDDLE EAST AND AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY AGE GROUP, 2018-2032 (USD MILLION)

TABLE 34 MIDDLE EAST AND AFRICA PEDIATRIC IN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY REGION, 2018-2032(USD MILLION)

TABLE 35 MIDDLE EAST AND AFRICA ADULT IN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY REGION, 2018-2032 (USD MILLION)

TABLE 36 MIDDLE EAST AND AFRICA GERIATRIC IN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY REGION, 2018-2032 (USD MILLION)

TABLE 37 MIDDLE EAST AND AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY DISTRIBUTION CHANNEL, 2018-2032 (USD MILLION)

TABLE 38 MIDDLE EAST AND AFRICA HOSPITAL PHARMACIES IN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY REGION, 2018-2032(USD MILLION)

TABLE 39 MIDDLE EAST AND AFRICA DRUGS STORES AND RETAIL PHARMACIES IN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY REGION, 2018-2032 (USD MILLION)

TABLE 40 MIDDLE EAST AND AFRICA ONLINE PHARMACIES IN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY REGION, 2018-2032 (USD MILLION)

TABLE 41 MIDDLE EAST AND AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY ROUTE OF ADMINISTRATION, 2018-2032 (USD MILLION)

TABLE 42 MIDDLE EAST AND AFRICA INTRAVENOUS (IV) IN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY REGION, 2018-2032(USD MILLION)

TABLE 43 MIDDLE EAST AND AFRICA SUBCUTANEOUS (SC) IN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY REGION, 2018-2032 (USD MILLION)

TABLE 44 MIDDLE EAST AND AFRICA ORAL IN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY REGION, 2018-2032 (USD MILLION)

TABLE 45 MIDDLE EAST AND AFRICA OTHERS IN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY REGION, 2018-2032 (USD MILLION)

TABLE 46 MIDDLE EAST AND AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY COUNTRY, 2018-2032 (USD MILLION)

TABLE 47 MIDDLE EAST AND AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY TYPE OF DISORDER, 2018-2032 (USD MILLION)

TABLE 48 MIDDLE EAST AND AFRICA GAUCHER DISEASE IN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY TYPE, 2018-2032 (USD MILLION)

TABLE 49 MIDDLE EAST AND AFRICA POMPE DISEASE IN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY TYPE, 2018-2032 (USD MILLION)

TABLE 50 MIDDLE EAST AND AFRICA MUCOPOLYSACCHARIDOSIS (MPS) IN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY TYPE, 2018-2032 (USD MILLION)

TABLE 51 MIDDLE EAST AND AFRICA NIEMANN-PICK DISEASE IN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY TYPE, 2018-2032 (USD MILLION)

TABLE 52 MIDDLE EAST AND AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY TYPE, 2018-2032 (USD MILLION)

TABLE 53 MIDDLE EAST AND AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY DRUGS, 2018-2032 (USD MILLION)

TABLE 54 MIDDLE EAST AND AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY ROUTE OF ADMINISTRATION, 2018-2032 (USD MILLION)

TABLE 55 MIDDLE EAST AND AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY AGE GROUP, 2018-2032 (USD MILLION)

TABLE 56 MIDDLE EAST AND AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY GENDER, 2018-2032 (USD MILLION)

TABLE 57 MIDDLE EAST AND AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY DISTRIBUTION CHANNEL, 2018-2032 (USD MILLION)

TABLE 58 SAUDI ARABIA LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY TYPE OF DISORDER, 2018-2032 (USD MILLION)

TABLE 59 SAUDI ARABIA GAUCHER DISEASE IN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY TYPE, 2018-2032 (USD MILLION)

TABLE 60 SAUDI ARABIA POMPE DISEASE IN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY TYPE, 2018-2032 (USD MILLION)

TABLE 61 SAUDI ARABIA MUCOPOLYSACCHARIDOSIS (MPS) IN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY TYPE, 2018-2032 (USD MILLION)

TABLE 62 SAUDI ARABIA NIEMANN-PICK DISEASE IN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY TYPE, 2018-2032 (USD MILLION)

TABLE 63 SAUDI ARABIA LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY TYPE, 2018-2032 (USD MILLION)

TABLE 64 SAUDI ARABIA LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY DRUGS, 2018-2032 (USD MILLION)

TABLE 65 SAUDI ARABIA LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY ROUTE OF ADMINISTRATION, 2018-2032 (USD MILLION)

TABLE 66 SAUDI ARABIA LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY AGE GROUP, 2018-2032 (USD MILLION)

TABLE 67 SAUDI ARABIA LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY GENDER, 2018-2032 (USD MILLION)

TABLE 68 SAUDI ARABIA LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY DISTRIBUTION CHANNEL, 2018-2032 (USD MILLION)

TABLE 69 UNITED ARAB EMIRATES (UAE) LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY TYPE OF DISORDER, 2018-2032 (USD MILLION)

TABLE 70 UNITED ARAB EMIRATES (UAE) GAUCHER DISEASE IN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY TYPE, 2018-2032 (USD MILLION)

TABLE 71 UNITED ARAB EMIRATES (UAE) POMPE DISEASE IN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY TYPE, 2018-2032 (USD MILLION)

TABLE 72 UNITED ARAB EMIRATES (UAE) MUCOPOLYSACCHARIDOSIS (MPS) IN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY TYPE, 2018-2032 (USD MILLION)

TABLE 73 UNITED ARAB EMIRATES (UAE) NIEMANN-PICK DISEASE IN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY TYPE, 2018-2032 (USD MILLION)

TABLE 74 UNITED ARAB EMIRATES (UAE) LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY TYPE, 2018-2032 (USD MILLION)

TABLE 75 UNITED ARAB EMIRATES (UAE) LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY DRUGS, 2018-2032 (USD MILLION)

TABLE 76 UNITED ARAB EMIRATES (UAE) LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY ROUTE OF ADMINISTRATION, 2018-2032 (USD MILLION)

TABLE 77 UNITED ARAB EMIRATES (UAE) LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY AGE GROUP, 2018-2032 (USD MILLION)

TABLE 78 UNITED ARAB EMIRATES (UAE) LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY GENDER, 2018-2032 (USD MILLION)

TABLE 79 UNITED ARAB EMIRATES (UAE) LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY DISTRIBUTION CHANNEL, 2018-2032 (USD MILLION)

TABLE 80 SOUTH AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY TYPE OF DISORDER, 2018-2032 (USD MILLION)

TABLE 81 SOUTH AFRICA GAUCHER DISEASE IN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY TYPE, 2018-2032 (USD MILLION)

TABLE 82 SOUTH AFRICA POMPE DISEASE IN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY TYPE, 2018-2032 (USD MILLION)

TABLE 83 SOUTH AFRICA MUCOPOLYSACCHARIDOSIS (MPS) IN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY TYPE, 2018-2032 (USD MILLION)

TABLE 84 SOUTH AFRICA NIEMANN-PICK DISEASE IN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY TYPE, 2018-2032 (USD MILLION)

TABLE 85 SOUTH AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY TYPE, 2018-2032 (USD MILLION)

TABLE 86 SOUTH AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY DRUGS, 2018-2032 (USD MILLION)

TABLE 87 SOUTH AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY ROUTE OF ADMINISTRATION, 2018-2032 (USD MILLION)

TABLE 88 SOUTH AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY AGE GROUP, 2018-2032 (USD MILLION)

TABLE 89 SOUTH AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY GENDER, 2018-2032 (USD MILLION)

TABLE 90 SOUTH AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY DISTRIBUTION CHANNEL, 2018-2032 (USD MILLION)

TABLE 91 EGYPT LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY TYPE OF DISORDER, 2018-2032 (USD MILLION)

TABLE 92 EGYPT GAUCHER DISEASE IN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY TYPE, 2018-2032 (USD MILLION)

TABLE 93 EGYPT POMPE DISEASE IN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY TYPE, 2018-2032 (USD MILLION)

TABLE 94 EGYPT MUCOPOLYSACCHARIDOSIS (MPS) IN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY TYPE, 2018-2032 (USD MILLION)

TABLE 95 EGYPT NIEMANN-PICK DISEASE IN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY TYPE, 2018-2032 (USD MILLION)

TABLE 96 EGYPT LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY TYPE, 2018-2032 (USD MILLION)

TABLE 97 EGYPT LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY DRUGS, 2018-2032 (USD MILLION)

TABLE 98 EGYPT LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY ROUTE OF ADMINISTRATION, 2018-2032 (USD MILLION)

TABLE 99 EGYPT LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY AGE GROUP, 2018-2032 (USD MILLION)

TABLE 100 EGYPT LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY GENDER, 2018-2032 (USD MILLION)

TABLE 101 EGYPT LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY DISTRIBUTION CHANNEL, 2018-2032 (USD MILLION)

TABLE 102 QATAR LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY TYPE OF DISORDER, 2018-2032 (USD MILLION)

TABLE 103 QATAR GAUCHER DISEASE IN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY TYPE, 2018-2032 (USD MILLION)

TABLE 104 QATAR POMPE DISEASE IN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY TYPE, 2018-2032 (USD MILLION)

TABLE 105 QATAR MUCOPOLYSACCHARIDOSIS (MPS) IN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY TYPE, 2018-2032 (USD MILLION)

TABLE 106 QATAR NIEMANN-PICK DISEASE IN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY TYPE, 2018-2032 (USD MILLION)

TABLE 107 QATAR LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY TYPE, 2018-2032 (USD MILLION)

TABLE 108 QATAR LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY DRUGS, 2018-2032 (USD MILLION)

TABLE 109 QATAR LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY ROUTE OF ADMINISTRATION, 2018-2032 (USD MILLION)

TABLE 110 QATAR LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY AGE GROUP, 2018-2032 (USD MILLION)

TABLE 111 QATAR LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY GENDER, 2018-2032 (USD MILLION)

TABLE 112 QATAR LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY DISTRIBUTION CHANNEL, 2018-2032 (USD MILLION)

TABLE 113 KUWAIT LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY TYPE OF DISORDER, 2018-2032 (USD MILLION)

TABLE 114 KUWAIT GAUCHER DISEASE IN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY TYPE, 2018-2032 (USD MILLION)

TABLE 115 KUWAIT POMPE DISEASE IN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY TYPE, 2018-2032 (USD MILLION)

TABLE 116 KUWAIT MUCOPOLYSACCHARIDOSIS (MPS) IN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY TYPE, 2018-2032 (USD MILLION)

TABLE 117 KUWAIT NIEMANN-PICK DISEASE IN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY TYPE, 2018-2032 (USD MILLION)

TABLE 118 KUWAIT LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY TYPE, 2018-2032 (USD MILLION)

TABLE 119 KUWAIT LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY DRUGS, 2018-2032 (USD MILLION)

TABLE 120 KUWAIT LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY ROUTE OF ADMINISTRATION, 2018-2032 (USD MILLION)

TABLE 121 KUWAIT LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY AGE GROUP, 2018-2032 (USD MILLION)

TABLE 122 KUWAIT LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY GENDER, 2018-2032 (USD MILLION)

TABLE 123 KUWAIT LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY DISTRIBUTION CHANNEL, 2018-2032 (USD MILLION)

TABLE 124 OMAN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY TYPE OF DISORDER, 2018-2032 (USD MILLION)

TABLE 125 OMAN GAUCHER DISEASE IN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY TYPE, 2018-2032 (USD MILLION)

TABLE 126 OMAN POMPE DISEASE IN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY TYPE, 2018-2032 (USD MILLION)

TABLE 127 OMAN MUCOPOLYSACCHARIDOSIS (MPS) IN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY TYPE, 2018-2032 (USD MILLION)

TABLE 128 OMAN NIEMANN-PICK DISEASE IN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY TYPE, 2018-2032 (USD MILLION)

TABLE 129 OMAN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY TYPE, 2018-2032 (USD MILLION)

TABLE 130 OMAN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY DRUGS, 2018-2032 (USD MILLION)

TABLE 131 OMAN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY ROUTE OF ADMINISTRATION, 2018-2032 (USD MILLION)

TABLE 132 OMAN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY AGE GROUP, 2018-2032 (USD MILLION)

TABLE 133 OMAN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY GENDER, 2018-2032 (USD MILLION)

TABLE 134 OMAN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY DISTRIBUTION CHANNEL, 2018-2032 (USD MILLION)

TABLE 135 BAHRAIN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY TYPE OF DISORDER, 2018-2032 (USD MILLION)

TABLE 136 BAHRAIN GAUCHER DISEASE IN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY TYPE, 2018-2032 (USD MILLION)

TABLE 137 BAHRAIN POMPE DISEASE IN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY TYPE, 2018-2032 (USD MILLION)

TABLE 138 BAHRAIN MUCOPOLYSACCHARIDOSIS (MPS) IN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY TYPE, 2018-2032 (USD MILLION)

TABLE 139 BAHRAIN NIEMANN-PICK DISEASE IN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY TYPE, 2018-2032 (USD MILLION)

TABLE 140 BAHRAIN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY TYPE, 2018-2032 (USD MILLION)

TABLE 141 BAHRAIN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY DRUGS, 2018-2032 (USD MILLION)

TABLE 142 BAHRAIN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY ROUTE OF ADMINISTRATION, 2018-2032 (USD MILLION)

TABLE 143 BAHRAIN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY AGE GROUP, 2018-2032 (USD MILLION)

TABLE 144 BAHRAIN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY GENDER, 2018-2032 (USD MILLION)

TABLE 145 BAHRAIN LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY DISTRIBUTION CHANNEL, 2018-2032 (USD MILLION)

TABLE 146 REST OF MIDDLE EAST AND AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY TYPE OF DISORDER, 2018-2032 (USD MILLION)

图片列表

FIGURE 1 MIDDLE EAST AND AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET: SEGMENTATION

FIGURE 2 MIDDLE EAST AND AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET: DATA TRIANGULATION

FIGURE 3 MIDDLE EAST AND AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET: DROC ANALYSIS

FIGURE 4 MIDDLE EAST AND AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET: MIDDLE EAST AND AFRICA VS REGIONAL MARKET ANALYSIS

FIGURE 5 MIDDLE EAST AND AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET: COMPANY RESEARCH ANALYSIS

FIGURE 6 MIDDLE EAST AND AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET: MULTIVARIATE MODELLING

FIGURE 7 MIDDLE EAST AND AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET: INTERVIEW DEMOGRAPHICS

FIGURE 8 MIDDLE EAST AND AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET: DBMR MARKET POSITION GRID

FIGURE 9 MIDDLE EAST AND AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET: SEGMENTATION

FIGURE 10 EXECUTIVE SUMMARY

FIGURE 11 SEVEN SEGMENTS COMPRISE THE MIDDLE EAST AND AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET, BY TYPE OF DISORDER

FIGURE 12 STRATEGIC DECISIONS

FIGURE 13 BIOTECHNOLOGY ADVANCEMENTS FOR LYSOSOMAL STORAGE DISORDER TREATMENTS IS EXPECTED TO DRIVE THE MIDDLE EAST AND AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET IN THE FORECAST PERIOD

FIGURE 14 GAUCHER DISEASE SEGMENT IS EXPECTED TO ACCOUNT FOR THE LARGEST SHARE OF THE MIDDLE EAST AND AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET IN 2025 & 2032

FIGURE 15 PESTEL ANALYSIS

FIGURE 16 DRIVERS, RESTRAINTS, OPPORTUNITIES AND CHALLENGES OF MIDDLE EAST AND AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET

FIGURE 17 MIDDLE EAST AND AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET: BY TYPE OF DISORDER, 2024

FIGURE 18 MIDDLE EAST AND AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET: BY TYPE OF DISORDER, 2025-2032 (USD MILLION)

FIGURE 19 MIDDLE EAST AND AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET: BY TYPE OF DISORDER, CAGR (2025-2032)

FIGURE 20 MIDDLE EAST AND AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET: BY TYPE OF DISORDER, LIFELINE CURVE

FIGURE 21 MIDDLE EAST AND AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET: BY DRUGS, 2024

FIGURE 22 MIDDLE EAST AND AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET: BY DRUGS, 2025-2032 (USD MILLION)

FIGURE 23 MIDDLE EAST AND AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET: BY DRUGS, CAGR (2025-2032)

FIGURE 24 MIDDLE EAST AND AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET: BY DRUGS, LIFELINE CURVE

FIGURE 25 MIDDLE EAST AND AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET: BY TYPE, 2024

FIGURE 26 MIDDLE EAST AND AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET: BY TYPE, 2025-2032 (USD MILLION)

FIGURE 27 MIDDLE EAST AND AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET: BY TYPE, CAGR (2025-2032)

FIGURE 28 MIDDLE EAST AND AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET: BY TYPE, LIFELINE CURVE

FIGURE 29 MIDDLE EAST AND AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET: BY GENDER, 2024

FIGURE 30 MIDDLE EAST AND AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET: BY GENDER, 2025-2032 (USD MILLION)

FIGURE 31 MIDDLE EAST AND AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET: BY GENDER, CAGR (2025-2032)

FIGURE 32 MIDDLE EAST AND AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET: BY GENDER, LIFELINE CURVE

FIGURE 33 MIDDLE EAST AND AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET: BY AGE GROUP, 2024

FIGURE 34 MIDDLE EAST AND AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET: BY AGE GROUP, 2025-2032 (USD MILLION)

FIGURE 35 MIDDLE EAST AND AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET: BY AGE GROUP, CAGR (2025-2032)

FIGURE 36 MIDDLE EAST AND AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET: BY AGE GROUP, LIFELINE CURVE

FIGURE 37 MIDDLE EAST AND AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET: BY DISTRIBUTION CHANNEL, 2024

FIGURE 38 MIDDLE EAST AND AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET: BY DISTRIBUTION CHANNEL, 2025-2032 (USD MILLION)

FIGURE 39 MIDDLE EAST AND AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET: BY DISTRIBUTION CHANNEL, CAGR (2025-2032)

FIGURE 40 MIDDLE EAST AND AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET: BY DISTRIBUTION CHANNEL, LIFELINE CURVE

FIGURE 41 MIDDLE EAST AND AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET: BY ROUTE OF ADMINISTRATION, 2024

FIGURE 42 MIDDLE EAST AND AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET: BY ROUTE OF ADMINISTRATION, 2025-2032 (USD MILLION)

FIGURE 43 MIDDLE EAST AND AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET: BY ROUTE OF ADMINISTRATION, CAGR (2025-2032)

FIGURE 44 MIDDLE EAST AND AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET: BY ROUTE OF ADMINISTRATION, LIFELINE CURVE

FIGURE 45 MIDDLE EAST AND AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET: SNAPSHOT 2024

FIGURE 46 MIDDLE EAST AND AFRICA LYSOSOMAL STORAGE DISORDER DRUGS MARKET: COMPANY SHARE 2024 (%)

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研究方法

数据收集和基准年分析是使用具有大样本量的数据收集模块完成的。该阶段包括通过各种来源和策略获取市场信息或相关数据。它包括提前检查和规划从过去获得的所有数据。它同样包括检查不同信息源中出现的信息不一致。使用市场统计和连贯模型分析和估计市场数据。此外,市场份额分析和关键趋势分析是市场报告中的主要成功因素。要了解更多信息,请请求分析师致电或下拉您的询问。

DBMR 研究团队使用的关键研究方法是数据三角测量,其中包括数据挖掘、数据变量对市场影响的分析和主要(行业专家)验证。数据模型包括供应商定位网格、市场时间线分析、市场概览和指南、公司定位网格、专利分析、定价分析、公司市场份额分析、测量标准、全球与区域和供应商份额分析。要了解有关研究方法的更多信息,请向我们的行业专家咨询。

可定制

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Frequently Asked Questions

市场是基于 中東和非洲溶小體貯積症藥物市場細分,按疾病類型(戈謝氏症、法布瑞氏症、龐貝氏症、黏多醣貯積症 (MPS)、尼曼匹克症、克拉伯氏症等)、類型(酵素替代療法 (ERT)、底物減少療法(SRT)、分子伴侶療法等)、藥物(伊米苷酶、阿加糖苷酶β、艾杜爾硫酸酶、阿葡糖苷酶α、維拉苷酶、塔利苷酶阿爾法、拉羅尼酶、阿加糖苷酶β、加洛硫酸酶、阿伐葡萄糖苷酶阿爾法靜脈注射 (IV)、皮下(SC)、口服等)、年齡層(兒科、成人和老年人)、性別(男性和女性)、分銷管道(醫院藥房、藥局)零售藥局和線上藥局)-產業趨勢及 2032 年預測 进行细分的。
在2024年,中東和非洲溶小體貯積症藥物市場的规模估计为510.05 USD Million美元。
中東和非洲溶小體貯積症藥物市場预计将在2025年至2032年的预测期内以CAGR 7.8%的速度增长。
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