North America Leber Congenital Amaurosis Market – Industry Trends and Forecast to 2029

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North America Leber Congenital Amaurosis Market – Industry Trends and Forecast to 2029

  • Pharmaceutical
  • Published Report
  • Apr 2022
  • North America
  • 350 Pages
  • No of Tables: 83
  • No of Figures: 37

Table of Content

1 INTRODUCTION

1.1 OBJECTIVES OF THE STUDY

1.2 MARKET DEFINITION

1.3 OVERVIEW OF NORTH AMERICA LEBER CONGENITAL AMAUROSIS MARKET

1.4 LIMITATIONS

1.5 MARKETS COVERED

2 MARKET SEGMENTATION

2.1 MARKETS COVERED

2.2 GEOGRAPHICAL SCOPE

2.3 YEARS CONSIDERED FOR THE STUDY

2.4 CURRENCY AND PRICING

2.5 DBMR TRIPOD DATA VALIDATION MODEL

2.6 MULTIVARIATE MODELLING

2.7 DISEASE TYPE LIFELINE CURVE

2.8 PRIMARY INTERVIEWS WITH KEY OPINION LEADERS

2.9 DBMR MARKET POSITION GRID

2.1 MARKET END USER COVERAGE GRID

2.11 VENDOR SHARE ANALYSIS

2.12 SECONDARY SOURCES

2.13 ASSUMPTIONS

3 EXECUTIVE SUMMARY

4 PREMIUM INSIGHTS

4.1 PIPELINE ANALYSIS FOR NORTH AMERICA LEBER CONGENTIAL AMAUROSIS MARKET

4.2 NORTH AMERICA LEBER CONGENITAL AMAUROSIS MARKET: REGULATIONS

4.3 PESTEL ANALYSIS

4.4 PORTERS FIVE FORCES

5 EPIDEMIOLOGY

6 NORTH AMERICA LEBER CONGENITAL AMAUROSIS MARKET, MARKET OVERVIEW

6.1 DRIVERS

6.1.1 INCREASE IN INCIDENCE AND PREVALENCE OF RPE65 GENE-MEDIATED IN RETINAL DISEASES

6.1.2 INCREASE IN PIPELINE PRODUCTS AND CLINICAL TRIALS

6.1.3 INCREASE IN STRATEGIC INITIATIVE BY KEY PLAYER

6.2 RESTRAINTS

6.2.1 LACK OF QUALIFIED PROFESSIONALS

6.2.2 HIGH COSTS ASSOCIATED WITH TREATMENT AND PROCEDURE

6.3 OPPORTUNITIES

6.3.1 INCREASE IN GOVERNMENT INITIATIVES TOWARD LEBER CONGENITAL AMAUROSIS

6.3.2 INCREASE IN THE TREATMENT-SEEKING RATE

6.3.3 FAVOURABLE REIMBURSEMENT POLICIES FOR THE TREATMENT

6.4 CHALLENGES

6.4.1 RISKS ASSOCIATED WITH LEBER CONGENITAL AMAUROSIS GENE THERAPY

6.4.2 STRINGENT GOVERNMENT REGULATIONS FOR GENE THERAPY PRODUCTS

7 NORTH AMERICA LEBER CONGENITAL AMAUROSIS MARKET, BY DISEASE TYPE

7.1 OVERVIEW

7.2 INFANTILE TYPE

7.3 JUVENILE TYPE

7.4 OTHERS

8 NORTH AMERICA LEBER CONGENITAL AMAUROSIS MARKET, BY TYPE

8.1 OVERVIEW

8.2 THERAPY

8.2.1 GENE THERAPY

8.2.1.1 LUXTURNA

8.2.2 RETINAL PROSTHETIC

8.2.3 NEUROPROTECTIVE AGENTS

8.2.3.1 VITAMIN A PALMITATE

8.2.3.2 DOCOSAHEXAENOIC ACID

8.2.3.3 LUTEIN

8.2.3.4 OTHERS

8.2.4 OTHERS

8.3 DIAGNOSIS

8.3.1 CLINICAL DIAGNOSIS

8.3.1.1 ELECTROPHYSIOLOGICAL TESTS

8.3.1.1.1 FULL-FIELD ELECTRORETINOGRAM (ERG)

8.3.1.1.2 DARK ADAPTOMETRY (DA)

8.3.1.2 RETINAL IMAGING

8.3.1.2.1 OPTICAL COHERENCE TOMOGRAPHY (OCT)

8.3.1.2.2 FUNDUS AUTOFLUORESCENCE

8.3.1.2.3 SCANNING LASER OPHTHALMOSCOPY (SLO)

8.3.1.2.4 ADAPTIVE OPTICS (AO) IMAGING

8.3.1.2.5 CONVENTIONAL COLOR FUNDUS IMAGING

8.3.1.3 VISUAL FIELD TEST

8.3.1.3.1 COMPUTERIZED VISUAL FIELD TESTS

8.3.1.3.2 MANUAL FIELD TEST

8.3.1.4 CLINICAL EYE EXAMINATION

8.3.1.4.1 SLIT LAMP

8.3.1.4.2 INDIRECT OPHTHALMOSCOPY

8.3.1.4.3 REFRACTION TEST

8.3.1.4.4 DILATION EXAM

8.3.1.5 OTHERS

8.3.2 GENETIC DIAGNOSIS

9 NORTH AMERICA LEBER CONGENITAL AMAUROSIS MARKET, BY END USER

9.1 OVERVIEW

9.2 HOSPITALS

9.3 SPECIALITY CLINICS

9.4 AMBULATORY SURGICAL CENTERS

9.5 HOME HEALTHCARE

9.6 OTHERS

10 NORTH AMERICA LEBER CONGENITAL AMAUROSIS MARKET, BY DISTRIBUTION CHANNEL

10.1 OVERVIEW

10.2 RETAIL SALES

10.2.1.1 HOSPITAL PHARMACIES

10.2.1.2 RETAIL PHARMACIES

10.2.1.3 OTHERS

10.3 DIRECT TENDER

11 NORTH AMERICA LEBER CONGENITAL AMAUROSIS MARKET, BY REGION

11.1 NORTH AMERICA

11.1.1 U.S.

11.1.2 CANADA

11.1.3 MEXICO

12 NORTH AMERICA LEBER CONGENITAL AMAUROSIS MARKET: COMPANY LANDSCAPE

12.1 COMPANY SHARE ANALYSIS: NORTH AMERICA

13 SWOT ANALYSIS

14 COMPANY PROFILE

14.1 SPARK THERAPEUTICS, INC

14.1.1 COMPANY SNAPSHOT

14.1.2 COMPANY SHARE ANALYSIS

14.1.3 PRODUCT PORTFOLIO

14.1.4 RECENT DEVELOPMENT

14.1.4.1 EU AUTHORIZATION

14.2 OPTOS

14.2.1 COMPANY SNAPSHOT

14.2.2 COMPANY SHARE ANALYSIS

14.2.3 PRODUCT PORTFOLIO

14.2.4 RECENT DEVELOPMENT

14.2.4.1 PRODUCT APPROVAL

14.3 CD GENOMICS

14.3.1 COMPANY SNAPSHOT

14.3.2 COMPANY SHARE ANALYSIS

14.3.3 PRODUCT PORTFOLIO

14.3.4 RECENT DEVELOPMENT

14.4 BLUEPRINTS GENETICS OY (A SUBSIDIARY OF QUEST DIAGNOSTICS)

14.4.1 COMPANY SNAPSHOT

14.4.2 REVENUE ANALYSIS

14.4.3 COMPANY SHARE ANALYSIS

14.4.4 PRODUCT PORTFOLIO

14.4.5 RECENT DEVELOPMENTS

14.4.5.1 COLLABORATION

14.5 LKC TECHNOLOGIES, INC

14.5.1 COMPANY SNAPSHOT

14.5.2 COMPANY SHARE ANALYSIS

14.5.3 PRODUCT PORTFOLIO

14.5.4 RECENT DEVELOPMENT

14.5.4.1 PRODUCT APPROVAL

14.5.5 PRODUCT APPROVAL

14.6 AGTC

14.6.1 COMPANY SNAPSHOT

14.6.2 REVENUE ANALYSIS

14.6.3 PRODUCT PORTFOLIO

14.6.4 RECENT DEVELOPMENTS

14.6.4.1 AGREEMENT

14.7 ALLERGAN (A SUBSIDIARY OF ABBVIE INC.)

14.7.1 COMPANY SNAPSHOT

14.7.2 REVENUE ANALYSIS

14.7.3 PRODUCT PORTFOLIO

14.7.4 RECENT DEVELOPMENTS

14.8 ASTELLAS PHARMA INC.

14.8.1 COMPANY SNAPSHOT

14.8.2 REVENUE ANALYSIS

14.8.3 PRODUCT PORTFOLIO

14.8.4 RECENT DEVELOPMENT

14.9 ATSENA THERAPEUTICS

14.9.1 COMPANY SNAPSHOT

14.9.2 PRODUCT PORTFOLIO

14.9.3 RECENT DEVELOPMENT

14.1 CENTOGENE N.V.

14.10.1 COMPANY SNAPSHOT

14.10.2 REVENUE ANALYSIS

14.10.3 PRODUCT PORTFOLIO

14.10.4 RECENT DEVELOPMENT

14.10.4.1 PRODUCT LAUNCH

14.11 COAVE THERAPEUTICS

14.11.1 COMPANY SNAPSHOT

14.11.2 PRODUCT PORTFOLIO

14.11.3 RECENT DEVELOPMENT

14.12 EDITAS MEDICINE

14.12.1 COMPANY SNAPSHOT

14.12.2 REVENUE ANALYSIS

14.12.3 PRODUCT PORTFOLIO

14.12.4 RECENT DEVELOPMENTS

14.12.4.1 DATA & TRAIL DATA PRESENTATION

14.13 ELUMINEX BIOSCIENCES

14.13.1 COMPANY SNAPSHOT

14.13.2 PRODUCT PORTFOLIO

14.13.3 RECENT DEVELOPMENT

14.14 GYROSCOPE THERAPEUTICS LIMITED

14.14.1 COMPANY SNAPSHOT

14.14.2 PRODUCT PORTFOLIO

14.14.3 RECENT DEVELOPMENTS

14.15 INVITAE CORPORATION

14.15.1 COMPANY SNAPSHOT

14.15.2 REVENUE ANALYSIS

14.15.3 PRODUCT PORTFOLIO

14.15.4 RECENT DEVELOPMENTS

14.15.4.1 NEW FACILITY

14.15.4.2 EXPANSION

14.16 IVERIC BIO.

14.16.1 COMPANY SNAPSHOT

14.16.2 PRODUCT PORTFOLIO

14.16.3 RECENT DEVELOPMENT

14.17 KUBOTA PHARMACEUTICAL HOLDINGS CO., LTD.

14.17.1 COMPANY SNAPSHOT

14.17.2 REVENUE ANALYSIS

14.17.3 PRODUCT PORTFOLIO

14.17.4 RECENT DEVELOPMENTS

14.18 MEIRAGTX LIMITED

14.18.1 COMPANY SNAPSHOT

14.18.2 PRODUCT PORTFOLIO

14.18.3 RECENT DEVELOPMENT

14.19 METROVISION

14.19.1 COMPANY SNAPSHOT

14.19.2 PRODUCT PORTFOLIO

14.19.3 RECENT DEVELOPMENT

14.19.3.1 FDA CLEARANCE APPROVAL

14.2 OCUGEN INC.

14.20.1 COMPANY SNAPSHOT

14.20.2 PRODUCT PORTFOLIO

14.20.3 RECENT DEVELOPMENT

14.21 OKUVISION

14.21.1 COMPANY SNAPSHOT

14.21.2 PRODUCT PORTFOLIO

14.21.3 RECENT DEVELOPMENTS

14.21.3.1 APPROVAL

14.22 PROQR THERAPEUTICS

14.22.1 COMPANY SNAPSHOT

14.22.2 PRODUCT PORTFOLIO

14.22.3 RECENT DEVELOPMENTS

14.23 REGENXBIO INC.

14.23.1 COMPANY SNAPSHOT

14.23.2 REVENUE ANALYSIS

14.23.3 PRODUCT PORTFOLIO

14.23.4 RECENT DEVELOPMENTS

14.24 SPARINGVISION

14.24.1 COMPANY SNAPSHOT

14.24.2 PRODUCT PORTFOLIO

14.24.3 RECENT DEVELOPMENTS

15 QUESTIONNAIRE

16 RELATED REPORTS

List of Table

TABLE 1 NORTH AMERICA LEBER CONGENITAL AMAUROSIS MARKET, BY DISEASE TYPE, 2020-2029 (USD MILLION)

TABLE 2 NORTH AMERICA INFANTILE TYPE IN LEBER CONGENITAL AMAUROSIS MARKET, BY REGION, 2020-2029 (USD MILLION)

TABLE 3 NORTH AMERICA JUVENILE TYPE IN LEBER CONGENITAL AMAUROSIS MARKET, BY REGION, 2020-2029 (USD MILLION)

TABLE 4 NORTH AMERICA OTHERS IN LEBER CONGENITAL AMAUROSIS MARKET, BY REGION, 2020-2029 (USD MILLION)

TABLE 5 NORTH AMERICA LEBER CONGENITAL AMAUROSIS MARKET, BY TYPE, 2020-2029 (USD MILLION)

TABLE 6 NORTH AMERICA THERAPY IN LEBER CONGENITAL AMAUROSIS MARKET, BY REGION, 2020-2029 (USD MILLION)

TABLE 7 NORTH AMERICA THERAPY IN LEBER CONGENITAL AMAUROSIS MARKET, BY TYPE, 2020-2029 (USD MILLION)

TABLE 8 NORTH AMERICA GENE THERAPY IN LEBER CONGENITAL AMAUROSIS MARKET, BY TYPE, 2020-2029 (USD MILLION)

TABLE 9 NORTH AMERICA NEUROPROTECTIVE AGENTS IN LEBER CONGENITAL AMAUROSIS MARKET, BY TYPE, 2020-2029 (USD MILLION)

TABLE 10 NORTH AMERICA DIAGNOSIS IN LEBER CONGENITAL AMAUROSIS MARKET, BY REGION, 2020-2029 (USD MILLION)

TABLE 11 NORTH AMERICA DIAGNOSIS IN LEBER CONGENITAL AMAUROSIS MARKET, BY TYPE, 2020-2029 (USD MILLION)

TABLE 12 NORTH AMERICA CLINICAL DIAGNOSIS IN LEBER CONGENITAL AMAUROSIS MARKET, BY TYPE, 2020-2029 (USD MILLION)

TABLE 13 NORTH AMERICA ELECTROPHYSIOLOGICAL TESTS IN LEBER CONGENITAL AMAUROSIS MARKET, BY TYPE, 2020-2029 (USD MILLION)

TABLE 14 NORTH AMERICA RETINAL IMAGING IN LEBER CONGENITAL AMAUROSIS MARKET, BY TYPE, 2020-2029 (USD MILLION)

TABLE 15 NORTH AMERICA VISUAL FIELD TEST IN LEBER CONGENITAL AMAUROSIS MARKET, BY TYPE, 2020-2029 (USD MILLION)

TABLE 16 NORTH AMERICA CLINICAL EYE EXAMINATION IN LEBER CONGENITAL AMAUROSIS MARKET, BY TYPE, 2020-2029 (USD MILLION)

TABLE 17 NORTH AMERICA LEBER CONGENITAL AMAUROSIS MARKET, BY END USER, 2020-2029 (USD MILLION)

TABLE 18 NORTH AMERICA HOSPITALS IN LEBER CONGENITAL AMAUROSIS MARKET, BY REGION, 2020-2029 (USD MILLION)

TABLE 19 NORTH AMERICA SPECIALITY CLINICS IN LEBER CONGENITAL AMAUROSIS MARKET, BY REGION, 2020-2029 (USD MILLION)

TABLE 20 NORTH AMERICA AMBULATORY SURGICAL CENTERS IN LEBER CONGENITAL AMAUROSIS MARKET, BY REGION, 2020-2029 (USD MILLION)

TABLE 21 NORTH AMERICA HOME HEALTHCARE IN LEBER CONGENITAL AMAUROSIS MARKET, BY REGION, 2020-2029 (USD MILLION)

TABLE 22 NORTH AMERICA OTHERS IN LEBER CONGENITAL AMAUROSIS MARKET, BY REGION, 2020-2029 (USD MILLION)

TABLE 23 NORTH AMERICA LEBER CONGENITAL AMAUROSIS MARKET, BY DISTRIBUTION CHANNEL, 2020-2029 (USD MILLION)

TABLE 24 NORTH AMERICA RETAIL SALES IN LEBER CONGENITAL AMAUROSIS MARKET, BY REGION, 2020-2029 (USD MILLION)

TABLE 25 NORTH AMERICA RETAIL SALES IN LEBER CONGENITAL AMAUROSIS MARKET, BY DISTRIBUTION CHANNEL, 2020-2029 (USD MILLION)

TABLE 26 NORTH AMERICA DIRECT TENDER IN LEBER CONGENITAL AMAUROSIS MARKET, BY REGION, 2020-2029 (USD MILLION)

TABLE 27 NORTH AMERICA LEBER CONGENITAL AMAUROSIS MARKET, BY COUNTRY, 2022-2029 (USD MILLION)

TABLE 28 NORTH AMERICA LEBER CONGENITAL AMAUROSIS MARKET, BY DISEASE TYPE, 2020-2029 (USD MILLION)

TABLE 29 NORTH AMERICA LEBER CONGENITAL AMAUROSIS MARKET, BY TYPE, 2020-2029 (USD MILLION)

TABLE 30 NORTH AMERICA THERAPY IN LEBER CONGENITAL AMAUROSIS MARKET, BY TYPE, 2020-2029 (USD MILLION)

TABLE 31 NORTH AMERICA GENE THERAPY IN LEBER CONGENITAL AMAUROSIS MARKET, BY TYPE, 2020-2029 (USD MILLION)

TABLE 32 NORTH AMERICA NEUROPROTECTIVE AGENTS IN LEBER CONGENITAL AMAUROSIS MARKET, BY TYPE, 2020-2029 (USD MILLION)

TABLE 33 NORTH AMERICA DIAGNOSIS IN LEBER CONGENITAL AMAUROSIS MARKET, BY TYPE, 2020-2029 (USD MILLION)

TABLE 34 NORTH AMERICA CLINICAL DIAGNOSIS IN LEBER CONGENITAL AMAUROSIS MARKET, BY TYPE, 2020-2029 (USD MILLION)

TABLE 35 NORTH AMERICA RETINAL IMAGING IN LEBER CONGENITAL AMAUROSIS MARKET, BY TYPE, 2020-2029 (USD MILLION)

TABLE 36 NORTH AMERICA ELECTROPHYSIOLOGICAL TESTS IN LEBER CONGENITAL AMAUROSIS MARKET, BY TYPE, 2020-2029 (USD MILLION)

TABLE 37 NORTH AMERICA VISUAL FIELD TEST IN LEBER CONGENITAL AMAUROSIS MARKET, BY TYPE, 2020-2029 (USD MILLION)

TABLE 38 NORTH AMERICA CLINICAL EYE EXAMINATION IN LEBER CONGENITAL AMAUROSIS MARKET, BY TYPE, 2020-2029 (USD MILLION)

TABLE 39 NORTH AMERICA LEBER CONGENITAL AMAUROSIS MARKET, BY END USER, 2020-2029 (USD MILLION)

TABLE 40 NORTH AMERICA LEBER CONGENITAL AMAUROSIS MARKET, BY DISTRIBUTION CHANNEL, 2020-2029 (USD MILLION)

TABLE 41 NORTH AMERICA RETAIL SALES IN LEBER CONGENITAL AMAUROSIS MARKET, BY DISTRIBUTION CHANNEL, 2020-2029 (USD MILLION)

TABLE 42 U.S. LEBER CONGENITAL AMAUROSIS MARKET, BY DISEASE TYPE, 2020-2029 (USD MILLION)

TABLE 43 U.S. LEBER CONGENITAL AMAUROSIS MARKET, BY TYPE, 2020-2029 (USD MILLION)

TABLE 44 U.S. THERAPY IN LEBER CONGENITAL AMAUROSIS MARKET, BY TYPE, 2020-2029 (USD MILLION)

TABLE 45 U.S. GENE THERAPY IN LEBER CONGENITAL AMAUROSIS MARKET, BY TYPE, 2020-2029 (USD MILLION)

TABLE 46 U.S. NEUROPROTECTIVE AGENTS IN LEBER CONGENITAL AMAUROSIS MARKET, BY TYPE, 2020-2029 (USD MILLION)

TABLE 47 U.S. DIAGNOSIS IN LEBER CONGENITAL AMAUROSIS MARKET, BY TYPE, 2020-2029 (USD MILLION)

TABLE 48 U.S. CLINICAL DIAGNOSIS IN LEBER CONGENITAL AMAUROSIS MARKET, BY TYPE, 2020-2029 (USD MILLION)

TABLE 49 U.S. RETINAL IMAGING IN LEBER CONGENITAL AMAUROSIS MARKET, BY TYPE, 2020-2029 (USD MILLION)

TABLE 50 U.S. ELECTROPHYSIOLOGICAL TESTS IN LEBER CONGENITAL AMAUROSIS MARKET, BY TYPE, 2020-2029 (USD MILLION)

TABLE 51 U.S. VISUAL FIELD TEST IN LEBER CONGENITAL AMAUROSIS MARKET, BY TYPE, 2020-2029 (USD MILLION)

TABLE 52 U.S. CLINICAL EYE EXAMINATION IN LEBER CONGENITAL AMAUROSIS MARKET, BY TYPE, 2020-2029 (USD MILLION)

TABLE 53 U.S. LEBER CONGENITAL AMAUROSIS MARKET, BY END USER, 2020-2029 (USD MILLION)

TABLE 54 U.S. LEBER CONGENITAL AMAUROSIS MARKET, BY DISTRIBUTION CHANNEL, 2020-2029 (USD MILLION)

TABLE 55 U.S. RETAIL SALES IN LEBER CONGENITAL AMAUROSIS MARKET, BY DISTRIBUTION CHANNEL, 2020-2029 (USD MILLION)

TABLE 56 CANADA LEBER CONGENITAL AMAUROSIS MARKET, BY DISEASE TYPE, 2020-2029 (USD MILLION)

TABLE 57 CANADA LEBER CONGENITAL AMAUROSIS MARKET, BY TYPE, 2020-2029 (USD MILLION)

TABLE 58 CANADA THERAPY IN LEBER CONGENITAL AMAUROSIS MARKET, BY TYPE, 2020-2029 (USD MILLION)

TABLE 59 CANADA GENE THERAPY IN LEBER CONGENITAL AMAUROSIS MARKET, BY TYPE, 2020-2029 (USD MILLION)

TABLE 60 CANADA NEUROPROTECTIVE AGENTS IN LEBER CONGENITAL AMAUROSIS MARKET, BY TYPE, 2020-2029 (USD MILLION)

TABLE 61 CANADA DIAGNOSIS IN LEBER CONGENITAL AMAUROSIS MARKET, BY TYPE, 2020-2029 (USD MILLION)

TABLE 62 CANADA CLINICAL DIAGNOSIS IN LEBER CONGENITAL AMAUROSIS MARKET, BY TYPE, 2020-2029 (USD MILLION)

TABLE 63 CANADA RETINAL IMAGING IN LEBER CONGENITAL AMAUROSIS MARKET, BY TYPE, 2020-2029 (USD MILLION)

TABLE 64 CANADA ELECTROPHYSIOLOGICAL TESTS IN LEBER CONGENITAL AMAUROSIS MARKET, BY TYPE, 2020-2029 (USD MILLION)

TABLE 65 CANADA VISUAL FIELD TEST IN LEBER CONGENITAL AMAUROSIS MARKET, BY TYPE, 2020-2029 (USD MILLION)

TABLE 66 CANADA CLINICAL EYE EXAMINATION IN LEBER CONGENITAL AMAUROSIS MARKET, BY TYPE, 2020-2029 (USD MILLION)

TABLE 67 CANADA LEBER CONGENITAL AMAUROSIS MARKET, BY END USER, 2020-2029 (USD MILLION)

TABLE 68 CANADA LEBER CONGENITAL AMAUROSIS MARKET, BY DISTRIBUTION CHANNEL, 2020-2029 (USD MILLION)

TABLE 69 CANADA RETAIL SALES IN LEBER CONGENITAL AMAUROSIS MARKET, BY DISTRIBUTION CHANNEL, 2020-2029 (USD MILLION)

TABLE 70 MEXICO LEBER CONGENITAL AMAUROSIS MARKET, BY DISEASE TYPE, 2020-2029 (USD MILLION)

TABLE 71 MEXICO LEBER CONGENITAL AMAUROSIS MARKET, BY TYPE, 2020-2029 (USD MILLION)

TABLE 72 MEXICO THERAPY IN LEBER CONGENITAL AMAUROSIS MARKET, BY TYPE, 2020-2029 (USD MILLION)

TABLE 73 MEXICO GENE THERAPY IN LEBER CONGENITAL AMAUROSIS MARKET, BY TYPE, 2020-2029 (USD MILLION)

TABLE 74 MEXICO NEUROPROTECTIVE AGENTS IN LEBER CONGENITAL AMAUROSIS MARKET, BY TYPE, 2020-2029 (USD MILLION)

TABLE 75 MEXICO DIAGNOSIS IN LEBER CONGENITAL AMAUROSIS MARKET, BY TYPE, 2020-2029 (USD MILLION)

TABLE 76 MEXICO CLINICAL DIAGNOSIS IN LEBER CONGENITAL AMAUROSIS MARKET, BY TYPE, 2020-2029 (USD MILLION)

TABLE 77 MEXICO RETINAL IMAGING IN LEBER CONGENITAL AMAUROSIS MARKET, BY TYPE, 2020-2029 (USD MILLION)

TABLE 78 MEXICO ELECTROPHYSIOLOGICAL TESTS IN LEBER CONGENITAL AMAUROSIS MARKET, BY TYPE, 2020-2029 (USD MILLION)

TABLE 79 MEXICO VISUAL FIELD TEST IN LEBER CONGENITAL AMAUROSIS MARKET, BY TYPE, 2020-2029 (USD MILLION)

TABLE 80 MEXICO CLINICAL EYE EXAMINATION IN LEBER CONGENITAL AMAUROSIS MARKET, BY TYPE, 2020-2029 (USD MILLION)

TABLE 81 MEXICO LEBER CONGENITAL AMAUROSIS MARKET, BY END USER, 2020-2029 (USD MILLION)

TABLE 82 MEXICO LEBER CONGENITAL AMAUROSIS MARKET, BY DISTRIBUTION CHANNEL, 2020-2029 (USD MILLION)

TABLE 83 MEXICO RETAIL SALES IN LEBER CONGENITAL AMAUROSIS MARKET, BY DISTRIBUTION CHANNEL, 2020-2029 (USD MILLION)

List of Figure

FIGURE 1 NORTH AMERICA LEBER CONGENITAL AMAUROSIS MARKET: SEGMENTATION

FIGURE 2 NORTH AMERICA LEBER CONGENITAL AMAUROSIS MARKET: DATA TRIANGULATION

FIGURE 3 NORTH AMERICA LEBER CONGENITAL AMAUROSIS MARKET: DROC ANALYSIS

FIGURE 4 NORTH AMERICA LEBER CONGENITAL AMAUROSIS MARKET: NORTH AMERICA VS REGIONAL MARKET ANALYSIS

FIGURE 5 NORTH AMERICA LEBER CONGENITAL AMAUROSIS MARKET: COMPANY RESEARCH ANALYSIS

FIGURE 6 NORTH AMERICA LEBER CONGENITAL AMAUROSIS MARKET: INTERVIEW DEMOGRAPHICS

FIGURE 7 NORTH AMERICA LEBER CONGENITAL AMAUROSIS MARKET: DBMR MARKET POSITION GRID

FIGURE 8 NORTH AMERICA LEBER CONGENITAL AMAUROSIS MARKET: END USER GRID

FIGURE 9 NORTH AMERICA LEBER CONGENITAL AMAUROSIS MARKET: VENDOR SHARE ANALYSIS

FIGURE 10 NORTH AMERICA LEBER CONGENITAL AMAUROSIS MARKET: SEGMENTATION

FIGURE 11 RISING GOVERNMENT AWARENESS PROGRAMS ABOUT THE INHERITED RETINAL DISEASE IS EXPECTED TO DRIVE THE NORTH AMERICA LEBER CONGENITAL AMAUROSIS MARKET IN THE FORECAST PERIOD OF 2022 TO 2029

FIGURE 12 INFANTILE TYPE IS EXPECTED TO ACCOUNT FOR THE LARGEST SHARE OF THE NORTH AMERICA LEBER CONGENITAL AMAUROSIS MARKET IN 2022 & 2029

FIGURE 13 NORTH AMERICA IS EXPECTED TO DOMINATE THE NORTH AMERICA LEBER CONGENITAL AMAUROSIS MARKET IN THE FORECAST PERIOD OF 2022 TO 2029

FIGURE 14 DRIVERS, RESTRAINTS, OPPORTUNITIES, AND CHALLENGES FOR THE NORTH AMERICA LEBER CONGENITAL AMAUROSIS MARKET

FIGURE 15 PROPORTION OF RPE65 GENE MUTATION IN CLINICALLY DIAGNOSED LCA PATIENTS

FIGURE 16 NORTH AMERICA LEBER CONGENITAL AMAUROSIS MARKET: BY DISEASE TYPE, 2021

FIGURE 17 NORTH AMERICA LEBER CONGENITAL AMAUROSIS MARKET: BY DISEASE TYPE, 2022-2029 (USD MILLION)

FIGURE 18 NORTH AMERICA LEBER CONGENITAL AMAUROSIS MARKET: BY DISEASE TYPE, CAGR (2022-2029)

FIGURE 19 NORTH AMERICA LEBER CONGENITAL AMAUROSIS MARKET: BY DISEASE TYPE, LIFELINE CURVE

FIGURE 20 NORTH AMERICA LEBER CONGENITAL AMAUROSIS MARKET: BY TYPE, 2021

FIGURE 21 NORTH AMERICA LEBER CONGENITAL AMAUROSIS MARKET: BY TYPE, 2022-2029 (USD MILLION)

FIGURE 22 NORTH AMERICA LEBER CONGENITAL AMAUROSIS MARKET: BY TYPE, CAGR (2022-2029)

FIGURE 23 NORTH AMERICA LEBER CONGENITAL AMAUROSIS MARKET: BY TYPE, LIFELINE CURVE

FIGURE 24 NORTH AMERICA LEBER CONGENITAL AMAUROSIS MARKET: BY END USER, 2021

FIGURE 25 NORTH AMERICA LEBER CONGENITAL AMAUROSIS MARKET: BY END USER, 2022-2029 (USD MILLION)

FIGURE 26 NORTH AMERICA LEBER CONGENITAL AMAUROSIS MARKET: BY END USER, CAGR (2022-2029)

FIGURE 27 NORTH AMERICA LEBER CONGENITAL AMAUROSIS MARKET: BY END USER, LIFELINE CURVE

FIGURE 28 NORTH AMERICA LEBER CONGENITAL AMAUROSIS MARKET: BY DISTRIBUTION CHANNEL, 2021

FIGURE 29 NORTH AMERICA LEBER CONGENITAL AMAUROSIS MARKET: BY END USER, 2022-2029 (USD MILLION)

FIGURE 30 NORTH AMERICA LEBER CONGENITAL AMAUROSIS MARKET: BY END USER, CAGR (2022-2029)

FIGURE 31 NORTH AMERICA LEBER CONGENITAL AMAUROSIS MARKET: BY END USER, LIFELINE CURVE

FIGURE 32 NORTH AMERICA LEBER CONGENITAL AMAUROSIS MARKET: SNAPSHOT (2021)

FIGURE 33 NORTH AMERICA LEBER CONGENITAL AMAUROSIS MARKET: BY COUNTRY (2021)

FIGURE 34 NORTH AMERICA LEBER CONGENITAL AMAUROSIS MARKET: BY COUNTRY (2022 & 2029)

FIGURE 35 NORTH AMERICA LEBER CONGENITAL AMAUROSIS MARKET: BY COUNTRY (2021 & 2029)

FIGURE 36 NORTH AMERICA LEBER CONGENITAL AMAUROSIS MARKET: BY DISEASE TYPE (2022-2029)

FIGURE 37 NORTH AMERICA LEBER CONGENITAL AMAUROSIS MARKET: COMPANY SHARE 2021 (%)