Lysosomal storage disorders are inherited metabolic disorders marked by an abnormal accumulation of numerous harmful chemicals in the body's cells as a result of enzyme shortages. There are roughly 50 of these ailments in all, and they can affect the skeleton, brain, skin, heart, and central nervous system, among other bodily components. There are still more lysosomal storage disorders being discovered. While clinical trials for potential treatments for some of these disorders are presently underway, many lysosomal storage diseases currently lack an approved medication.
